Optimization of Lipoplexes Functionalized with a Sialic Acid Mimetic (F9-PEG) to Target the C1858T PTPN22 Variant for Preclinical Assessment of a Novel Immunotherapy in Endocrine Autoimmunity.

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Title: Optimization of Lipoplexes Functionalized with a Sialic Acid Mimetic (F9-PEG) to Target the C1858T PTPN22 Variant for Preclinical Assessment of a Novel Immunotherapy in Endocrine Autoimmunity.
Authors: Sennato S; CNR-Institute for Complex Systems (ISC), and Physics Department, Sapienza University of Rome, P. le A. Moro 5, 00185 Rome, Italy., Paldino G; Bambino Gesù Children's Hospital, Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS), 00146 Rome, Italy., Bombelli C; CNR-Institute for Biological Systems, Secondary Office of Rome-Sapienza University of Rome, 00185 Rome, Italy., Mezzani I; Bambino Gesù Children's Hospital, Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS), 00146 Rome, Italy., Petrini S; Bambino Gesù Children's Hospital, Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS), 00146 Rome, Italy., Belcastro E; Bambino Gesù Children's Hospital, Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS), 00146 Rome, Italy., Delfino DV; Department of Medicine and Surgery, University of Perugia, 06129 Perugia, Italy., Fiorentino F; Department of Drug Chemistry and Technologies, Sapienza University of Rome, 00185 Rome, Italy., Marianecci C; Department of Drug Chemistry and Technologies, Sapienza University of Rome, 00185 Rome, Italy., Ciogli A; Department of Drug Chemistry and Technologies, Sapienza University of Rome, 00185 Rome, Italy., Rotili D; Department of Science, Roma Tre University, 00146 Rome, Italy., Ceccacci F; CNR-Institute for Biological Systems, Secondary Office of Rome-Sapienza University of Rome, 00185 Rome, Italy., Fierabracci A; Bambino Gesù Children's Hospital, Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS), 00146 Rome, Italy.
Source: Pharmaceutics [Pharmaceutics] 2025 May 28; Vol. 17 (6). Date of Electronic Publication: 2025 May 28.
Publication Type: Journal Article
Journal Info: Publisher: MDPI Country of Publication: Switzerland NLM ID: 101534003 Publication Model: Electronic Cited Medium: Print ISSN: 1999-4923 (Print) Linking ISSN: 19994923 NLM ISO Abbreviation: Pharmaceutics Subsets: PubMed not MEDLINE
Database: MEDLINE Ultimate
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ISSN:1999-4923
DOI:10.3390/pharmaceutics17060710