Spinal Muscular Atrophy Functional Composite Score Revised (SMA-FCR) in Untreated and Nusinersen-Treated Patient Cohorts.

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Bibliographic Details
Title: Spinal Muscular Atrophy Functional Composite Score Revised (SMA-FCR) in Untreated and Nusinersen-Treated Patient Cohorts.
Authors: Pasternak A; Department of Physical and Occupational Therapy Services, Boston Children's Hospital, MA., McDermott MP; Department of Biostatistics and Compulational Biology, University of Rochester, NY., Montes J; Department of Rehabilitation and Regenerative Medicine, Columbia University Irving Medical Center, New York, NY., Glanzman AM; Department of Physical Therapy, Children's Hospital of Philadelphia, PA., Coratti G; Centro Clinico Nemo, U.O.C. Neuropsichiatria Infantile Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy., Dunaway Young S; Departments of Neurology and Clinical Neurosciences, Stanford University, Palo Alto, CA., Duong TT; Departments of Neurology and Clinical Neurosciences, Stanford University, Palo Alto, CA., Martens WB; Department of Neurology, University of Rochester, NY., Day JW; Departments of Neurology and Clinical Neurosciences, Stanford University, Palo Alto, CA., Zolkipli-Cunningham Z; Division of Human Genetics, Children's Hospital of Philadelphia, University of Philadelphia, PA., Sansone VA; The NEMO Center in Milan, Neurorehabilitation Unit, University of Milan, ASST Niguarda Hospital, Italy., D'Amico A; Unit of Neuromuscular and Neurodegenerative Disorders, IRCCS Bambino Gesu Children's Hospital, Rome, Italy., Messina S; Department of Clinical and Experimental Medicine and Centro Clinico Nemo Sud, University of Messina, Italy., Bruno C; Center of Experimental and Translational Myology, IRCCS Isituto Giannina Gaslini, Genoa, Italy., Mercuri E; Centro Clinico Nemo, U.O.C. Neuropsichiatria Infantile Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy., De Vivo DC; Department of Neurology, Columbia University Irving Medical Center, New York, NY; and., Darras BT; Department of Neurology, Boston Children's Hospital, Harvard Medical School, MA.
Corporate Authors: as the Pediatric Neuromuscular Clinical Research (PNCR) Network and the International SMA Consortium (iSMAc)
Source: Neurology [Neurology] 2025 Jul 22; Vol. 105 (2), pp. e213839. Date of Electronic Publication: 2025 Jun 27.
Publication Type: Journal Article
Journal Info: Publisher: Lippincott Williams & Wilkins Country of Publication: United States NLM ID: 0401060 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1526-632X (Electronic) Linking ISSN: 00283878 NLM ISO Abbreviation: Neurology Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1526-632X
DOI:10.1212/WNL.0000000000213839