Successful off-label use of elexacaftor/tezacaftor/ivacaftor in an infant with severe CF disease.

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Bibliographic Details
Title: Successful off-label use of elexacaftor/tezacaftor/ivacaftor in an infant with severe CF disease.
Authors: Shevill E; Department of Respiratory Medicine, Queensland Children's Hospital (QCH), Brisbane, Queensland, Australia., Wainwright CE; Department of Respiratory Medicine, Queensland Children's Hospital (QCH), Brisbane, Queensland, Australia; Child Health Research Centre, University of Queensland, Queensland, Australia., Churchett M; Department of Dietetics, Queensland Children's Hospital (QCH), Brisbane, Queensland, Australia., Sexton J; Department of Physiotherapy, Queensland Children's Hospital (QCH), Brisbane, Queensland, Australia., Irving H; Centre for Children's Health Ethics and Law, Queensland Children's Hospital (QCH), Brisbane, Queensland, Australia., Manoy S; Centre for Children's Health Ethics and Law, Queensland Children's Hospital (QCH), Brisbane, Queensland, Australia., Figgins S; Department of Pharmacy, Queensland Children's Hospital (QCH), Brisbane, Queensland, Australia., Swyer K; Department of Social Work, Queensland Children's Hospital (QCH), Brisbane, Queensland, Australia., Fazackerley LA; School of Exercise and Nutrition Sciences, Faculty of Health, Queensland University of Technology, Brisbane, Queensland, Australia., Robinson PD; Department of Respiratory Medicine, Queensland Children's Hospital (QCH), Brisbane, Queensland, Australia; Child Health Research Centre, University of Queensland, Queensland, Australia. Electronic address: paul.robinson@uq.edu.au.
Source: Journal of cystic fibrosis : official journal of the European Cystic Fibrosis Society [J Cyst Fibros] 2025 Sep; Vol. 24 (5), pp. 935-938. Date of Electronic Publication: 2025 Aug 18.
Publication Type: Case Reports; Journal Article
Journal Info: Publisher: Elsevier Country of Publication: Netherlands NLM ID: 101128966 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1873-5010 (Electronic) Linking ISSN: 15691993 NLM ISO Abbreviation: J Cyst Fibros Subsets: MEDLINE; In Process
Database: MEDLINE Ultimate
Description
ISSN:1873-5010
DOI:10.1016/j.jcf.2025.08.006