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Descriptive characterization of ambulatory health states in Duchenne muscular dystrophy: Motor function trajectories and times to loss of ambulation.

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Title: Descriptive characterization of ambulatory health states in Duchenne muscular dystrophy: Motor function trajectories and times to loss of ambulation.
Authors: Muntoni F; Dubowitz Neuromuscular Centre, Great Ormond Street Institute of Child Health, London, UK.; NIHR Great Ormond Street Hospital Biomedical Research Centre, London, UK., Signorovitch J; Analysis Group, Inc., Boston, MA, USA.; Collaborative Trajectory Analysis Project (cTAP), Cambridge, MA, USA., Johnson M; Analysis Group, Inc., Boston, MA, USA., Gomez-Lievano A; Analysis Group, Inc., Boston, MA, USA., Posner N; Pfizer, Inc., New York, NY, USA., Dorling P; Pfizer, Inc., New York, NY, USA., Beaverson K; Pfizer, Inc., New York, NY, USA., Alvir J; Pfizer, Inc., New York, NY, USA., Mahn M; Pfizer, Inc., New York, NY, USA., Ward SJ; Collaborative Trajectory Analysis Project (cTAP), Cambridge, MA, USA., Goemans N; Child Neurology, University Hospitals Leuven, Leuven, Belgium., Vandenborne K; University of Florida, Gainesville, FL, USA., Mercuri E; Pediatric Neurology, Catholic University, Rome, Italy.; Centro Clinico NeMO, Fondazione Policlinico Gemelli IRCCS, Rome, Italy., McDonald CM; Department of Physical Medicine and Rehabilitation, University of California, Sacramento, CA, USA.
Source: Journal of neuromuscular diseases [J Neuromuscul Dis] 2026 Jul; Vol. 13 (4), pp. 781-787. Date of Electronic Publication: 2025 Sep 23.
Publication Type: Journal Article
Journal Info: Publisher: IOS Press Country of Publication: United States NLM ID: 101649948 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2214-3602 (Electronic) Linking ISSN: 22143599 NLM ISO Abbreviation: J Neuromuscul Dis Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: <searchLink fieldCode="AU" term="%22Muntoni+F%22">Muntoni F</searchLink>; Dubowitz Neuromuscular Centre, Great Ormond Street Institute of Child Health, London, UK.; NIHR Great Ormond Street Hospital Biomedical Research Centre, London, UK.<br /><searchLink fieldCode="AU" term="%22Signorovitch+J%22">Signorovitch J</searchLink>; Analysis Group, Inc., Boston, MA, USA.; Collaborative Trajectory Analysis Project (cTAP), Cambridge, MA, USA.<br /><searchLink fieldCode="AU" term="%22Johnson+M%22">Johnson M</searchLink>; Analysis Group, Inc., Boston, MA, USA.<br /><searchLink fieldCode="AU" term="%22Gomez-Lievano+A%22">Gomez-Lievano A</searchLink>; Analysis Group, Inc., Boston, MA, USA.<br /><searchLink fieldCode="AU" term="%22Posner+N%22">Posner N</searchLink>; Pfizer, Inc., New York, NY, USA.<br /><searchLink fieldCode="AU" term="%22Dorling+P%22">Dorling P</searchLink>; Pfizer, Inc., New York, NY, USA.<br /><searchLink fieldCode="AU" term="%22Beaverson+K%22">Beaverson K</searchLink>; Pfizer, Inc., New York, NY, USA.<br /><searchLink fieldCode="AU" term="%22Alvir+J%22">Alvir J</searchLink>; Pfizer, Inc., New York, NY, USA.<br /><searchLink fieldCode="AU" term="%22Mahn+M%22">Mahn M</searchLink>; Pfizer, Inc., New York, NY, USA.<br /><searchLink fieldCode="AU" term="%22Ward+SJ%22">Ward SJ</searchLink>; Collaborative Trajectory Analysis Project (cTAP), Cambridge, MA, USA.<br /><searchLink fieldCode="AU" term="%22Goemans+N%22">Goemans N</searchLink>; Child Neurology, University Hospitals Leuven, Leuven, Belgium.<br /><searchLink fieldCode="AU" term="%22Vandenborne+K%22">Vandenborne K</searchLink>; University of Florida, Gainesville, FL, USA.<br /><searchLink fieldCode="AU" term="%22Mercuri+E%22">Mercuri E</searchLink>; Pediatric Neurology, Catholic University, Rome, Italy.; Centro Clinico NeMO, Fondazione Policlinico Gemelli IRCCS, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22McDonald+CM%22">McDonald CM</searchLink>; Department of Physical Medicine and Rehabilitation, University of California, Sacramento, CA, USA.
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  Data: <searchLink fieldCode="JN" term="%22101649948%22">Journal of neuromuscular diseases</searchLink> [J Neuromuscul Dis] 2026 Jul; Vol. 13 (4), pp. 781-787. <i>Date of Electronic Publication: </i>2025 Sep 23.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22IOS+Press%22">IOS Press </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101649948 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>2214-3602 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2222143599%22">22143599 </searchLink><i>NLM ISO Abbreviation: </i>J Neuromuscul Dis <i>Subsets: </i>MEDLINE
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        Value: 10.1177/22143602251364694
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              Text: 2026 Jul
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