Efficient Installation of Heterozygous Mutations in Human Pluripotent Stem Cells Using Prime Editing.

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Bibliographic Details
Title: Efficient Installation of Heterozygous Mutations in Human Pluripotent Stem Cells Using Prime Editing.
Authors: Suter A; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia., Graham A; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia., Kuah JY; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia., Crisologo J; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia., Gunatilake C; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia., Sourris K; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia., See M; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia., Rossello FJ; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia.; Department of Clinical Pathology, University of Melbourne, Melbourne, Australia.; Australian Regenerative Medicine Institute, Monash University, Victoria, Australia., Ramialison M; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia.; Australian Regenerative Medicine Institute, Monash University, Victoria, Australia.; Department of Paediatrics, University of Melbourne, Melbourne, Australia., Vlahos K; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia., Howden SE; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia.; Department of Paediatrics, University of Melbourne, Melbourne, Australia.; Lead contact.
Source: The CRISPR journal [CRISPR J] 2025 Dec; Vol. 8 (6), pp. 401-411. Date of Electronic Publication: 2025 Sep 24.
Publication Type: Journal Article
Journal Info: Publisher: Mary Ann Liebert, Inc Country of Publication: United States NLM ID: 101738191 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2573-1602 (Electronic) Linking ISSN: 25731599 NLM ISO Abbreviation: CRISPR J Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:2573-1602
DOI:10.1177/25731599251380122