Real-Life Efficacy and Safety of BRAF Inhibitors in Erdheim-Chester Disease.

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Title: Real-Life Efficacy and Safety of BRAF Inhibitors in Erdheim-Chester Disease.
Authors: Pegoraro F; Department of Experimental and Clinical Medicine, University of Florence, Florence, Italy.; Department of Hematology and Oncology, Meyer Children's Hospital IRCCS, Florence, Italy., Peyronel F; Department of Experimental and Clinical Medicine, University of Florence, Florence, Italy.; Nephrology and Dialysis Unit, Careggi University Hospital, Florence, Italy., Papo M; Departement of Internal Medicine 2, Center of reference of Histiocytosis, Hôpital Pitié-Salpêtrière, Sorbonne University, Assistance Publique-Hôpitaux de Paris, Paris, France., Sutera R; Departement of Internal Medicine 2, Center of reference of Histiocytosis, Hôpital Pitié-Salpêtrière, Sorbonne University, Assistance Publique-Hôpitaux de Paris, Paris, France.; School of Medicine, University of Florence, Florence, Italy., Catamerò F; Department of Health Sciences, University of Florence, Florence, Italy., Poeta F; Department of Health Sciences, University of Florence, Florence, Italy., Razanamahery J; Department of Internal Medicine and Clinical Immunology, Dijon University Hospital, Dijon, France., Ledoult E; Department of Internal Medicine, Lille University Hospital, Lille, France., Le Scornet T; Department of Internal Medicine, Nantes University Hospital, Nantes, France., de Menthon M; Department of Internal Medicine and Clinical Immunology, Bicetre Hospital, Assistance Publique - Hôpitaux de Paris, Le Kremlin Bicêtre, France., Riviere E; Department of Internal Medicine, Haut-Lévèque University Hospital, Bordeaux, France., Sieni E; Department of Hematology and Oncology, Meyer Children's Hospital IRCCS, Florence, Italy., Barete S; Department of Dermatology, CEREMAST, Pitié-Salpȇtrière Hospital, Sorbonne University, Assistance Publique-Hôpitaux de Paris, Paris, France., Idbaih A; Sorbonne Université, AP-HP, Institut du Cerveau - Paris Brain Institute - ICM, Inserm, CNRS, Hôpitaux Universitaires La Pitié Salpêtrière - Charles Foix, DMU Neurosciences, Service de Neuro-Oncologie-Institut de Neurologie, Paris, France., Cohen-Aubart F; Departement of Internal Medicine 2, Center of reference of Histiocytosis, Hôpital Pitié-Salpêtrière, Sorbonne University, Assistance Publique-Hôpitaux de Paris, Paris, France., Amoura Z; Departement of Internal Medicine 2, Center of reference of Histiocytosis, Hôpital Pitié-Salpêtrière, Sorbonne University, Assistance Publique-Hôpitaux de Paris, Paris, France., Emile JF; Department of Pathology, Ambroise Paré Hospital, EA4340 BECCOH, Versailles SQY University, Boulogne, France., Vaglio A; Department of Biomedical, Experimental and Clinical Sciences 'Mario Serio', University of Florence, Florence, Italy.; Nephrology and Dialysis Unit, Meyer Children's Hospital IRCCS, Florence, Italy., Haroche J; Departement of Internal Medicine 2, Center of reference of Histiocytosis, Hôpital Pitié-Salpêtrière, Sorbonne University, Assistance Publique-Hôpitaux de Paris, Paris, France.
Source: American journal of hematology [Am J Hematol] 2026 Jan; Vol. 101 (1), pp. 182-186. Date of Electronic Publication: 2025 Nov 08.
Publication Type: Letter
Journal Info: Publisher: Wiley-Blackwell Country of Publication: United States NLM ID: 7610369 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1096-8652 (Electronic) Linking ISSN: 03618609 NLM ISO Abbreviation: Am J Hematol Subsets: MEDLINE; In Process
Database: MEDLINE Ultimate
Description
ISSN:1096-8652
DOI:10.1002/ajh.70137