Exposure-Response Analysis of Donidalorsen for the Treatment of Hereditary Angioedema.

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Bibliographic Details
Title: Exposure-Response Analysis of Donidalorsen for the Treatment of Hereditary Angioedema.
Authors: Singh P; Ionis, Carlsbad, California, USA., Witjes H; Certara, Radnor, Pennsylvania, USA., Kleijn HJ; Certara, Radnor, Pennsylvania, USA., Diep JK; Ionis, Carlsbad, California, USA., Bordone L; Ionis, Carlsbad, California, USA., Newman KB; Ionis, Carlsbad, California, USA., Gao X; Ionis, Carlsbad, California, USA., Cohn DM; Department of Vascular Medicine, Amsterdam Cardiovascular Sciences, Amsterdam UMC, University of Amsterdam, Amsterdam, the Netherlands.
Source: Clinical and translational science [Clin Transl Sci] 2025 Nov; Vol. 18 (11), pp. e70388.
Publication Type: Clinical Trial, Phase III; Journal Article; Multicenter Study; Randomized Controlled Trial
Journal Info: Publisher: WileyBlackwell Pub Country of Publication: United States NLM ID: 101474067 Publication Model: Print Cited Medium: Internet ISSN: 1752-8062 (Electronic) Linking ISSN: 17528054 NLM ISO Abbreviation: Clin Transl Sci Subsets: MEDLINE
Database: MEDLINE Ultimate
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ISSN:1752-8062
DOI:10.1111/cts.70388