Exposure-Response Analysis of Donidalorsen for the Treatment of Hereditary Angioedema.
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| Title: | Exposure-Response Analysis of Donidalorsen for the Treatment of Hereditary Angioedema. |
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| Authors: | Singh P; Ionis, Carlsbad, California, USA., Witjes H; Certara, Radnor, Pennsylvania, USA., Kleijn HJ; Certara, Radnor, Pennsylvania, USA., Diep JK; Ionis, Carlsbad, California, USA., Bordone L; Ionis, Carlsbad, California, USA., Newman KB; Ionis, Carlsbad, California, USA., Gao X; Ionis, Carlsbad, California, USA., Cohn DM; Department of Vascular Medicine, Amsterdam Cardiovascular Sciences, Amsterdam UMC, University of Amsterdam, Amsterdam, the Netherlands. |
| Source: | Clinical and translational science [Clin Transl Sci] 2025 Nov; Vol. 18 (11), pp. e70388. |
| Publication Type: | Clinical Trial, Phase III; Journal Article; Multicenter Study; Randomized Controlled Trial |
| Journal Info: | Publisher: WileyBlackwell Pub Country of Publication: United States NLM ID: 101474067 Publication Model: Print Cited Medium: Internet ISSN: 1752-8062 (Electronic) Linking ISSN: 17528054 NLM ISO Abbreviation: Clin Transl Sci Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| ISSN: | 1752-8062 |
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| DOI: | 10.1111/cts.70388 |