Exposure-Response Analysis of Donidalorsen for the Treatment of Hereditary Angioedema.

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Title: Exposure-Response Analysis of Donidalorsen for the Treatment of Hereditary Angioedema.
Authors: Singh P; Ionis, Carlsbad, California, USA., Witjes H; Certara, Radnor, Pennsylvania, USA., Kleijn HJ; Certara, Radnor, Pennsylvania, USA., Diep JK; Ionis, Carlsbad, California, USA., Bordone L; Ionis, Carlsbad, California, USA., Newman KB; Ionis, Carlsbad, California, USA., Gao X; Ionis, Carlsbad, California, USA., Cohn DM; Department of Vascular Medicine, Amsterdam Cardiovascular Sciences, Amsterdam UMC, University of Amsterdam, Amsterdam, the Netherlands.
Source: Clinical and translational science [Clin Transl Sci] 2025 Nov; Vol. 18 (11), pp. e70388.
Publication Type: Clinical Trial, Phase III; Journal Article; Multicenter Study; Randomized Controlled Trial
Journal Info: Publisher: WileyBlackwell Pub Country of Publication: United States NLM ID: 101474067 Publication Model: Print Cited Medium: Internet ISSN: 1752-8062 (Electronic) Linking ISSN: 17528054 NLM ISO Abbreviation: Clin Transl Sci Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Exposure-Response Analysis of Donidalorsen for the Treatment of Hereditary Angioedema.
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  Data: <searchLink fieldCode="AU" term="%22Singh+P%22">Singh P</searchLink>; Ionis, Carlsbad, California, USA.<br /><searchLink fieldCode="AU" term="%22Witjes+H%22">Witjes H</searchLink>; Certara, Radnor, Pennsylvania, USA.<br /><searchLink fieldCode="AU" term="%22Kleijn+HJ%22">Kleijn HJ</searchLink>; Certara, Radnor, Pennsylvania, USA.<br /><searchLink fieldCode="AU" term="%22Diep+JK%22">Diep JK</searchLink>; Ionis, Carlsbad, California, USA.<br /><searchLink fieldCode="AU" term="%22Bordone+L%22">Bordone L</searchLink>; Ionis, Carlsbad, California, USA.<br /><searchLink fieldCode="AU" term="%22Newman+KB%22">Newman KB</searchLink>; Ionis, Carlsbad, California, USA.<br /><searchLink fieldCode="AU" term="%22Gao+X%22">Gao X</searchLink>; Ionis, Carlsbad, California, USA.<br /><searchLink fieldCode="AU" term="%22Cohn+DM%22">Cohn DM</searchLink>; Department of Vascular Medicine, Amsterdam Cardiovascular Sciences, Amsterdam UMC, University of Amsterdam, Amsterdam, the Netherlands.
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  Data: Clinical Trial, Phase III; Journal Article; Multicenter Study; Randomized Controlled Trial
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        Value: 10.1111/cts.70388
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      – Code: eng
        Text: English
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      – TitleFull: Exposure-Response Analysis of Donidalorsen for the Treatment of Hereditary Angioedema.
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              M: 11
              Text: 2025 Nov
              Type: published
              Y: 2025
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