Exposure-Response Analysis of Donidalorsen for the Treatment of Hereditary Angioedema.
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| Title: | Exposure-Response Analysis of Donidalorsen for the Treatment of Hereditary Angioedema. |
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| Authors: | Singh P; Ionis, Carlsbad, California, USA., Witjes H; Certara, Radnor, Pennsylvania, USA., Kleijn HJ; Certara, Radnor, Pennsylvania, USA., Diep JK; Ionis, Carlsbad, California, USA., Bordone L; Ionis, Carlsbad, California, USA., Newman KB; Ionis, Carlsbad, California, USA., Gao X; Ionis, Carlsbad, California, USA., Cohn DM; Department of Vascular Medicine, Amsterdam Cardiovascular Sciences, Amsterdam UMC, University of Amsterdam, Amsterdam, the Netherlands. |
| Source: | Clinical and translational science [Clin Transl Sci] 2025 Nov; Vol. 18 (11), pp. e70388. |
| Publication Type: | Clinical Trial, Phase III; Journal Article; Multicenter Study; Randomized Controlled Trial |
| Journal Info: | Publisher: WileyBlackwell Pub Country of Publication: United States NLM ID: 101474067 Publication Model: Print Cited Medium: Internet ISSN: 1752-8062 (Electronic) Linking ISSN: 17528054 NLM ISO Abbreviation: Clin Transl Sci Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| FullText | Links: – Type: pdflink Text: Availability: 1 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 41208217 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Exposure-Response Analysis of Donidalorsen for the Treatment of Hereditary Angioedema. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Singh+P%22">Singh P</searchLink>; Ionis, Carlsbad, California, USA.<br /><searchLink fieldCode="AU" term="%22Witjes+H%22">Witjes H</searchLink>; Certara, Radnor, Pennsylvania, USA.<br /><searchLink fieldCode="AU" term="%22Kleijn+HJ%22">Kleijn HJ</searchLink>; Certara, Radnor, Pennsylvania, USA.<br /><searchLink fieldCode="AU" term="%22Diep+JK%22">Diep JK</searchLink>; Ionis, Carlsbad, California, USA.<br /><searchLink fieldCode="AU" term="%22Bordone+L%22">Bordone L</searchLink>; Ionis, Carlsbad, California, USA.<br /><searchLink fieldCode="AU" term="%22Newman+KB%22">Newman KB</searchLink>; Ionis, Carlsbad, California, USA.<br /><searchLink fieldCode="AU" term="%22Gao+X%22">Gao X</searchLink>; Ionis, Carlsbad, California, USA.<br /><searchLink fieldCode="AU" term="%22Cohn+DM%22">Cohn DM</searchLink>; Department of Vascular Medicine, Amsterdam Cardiovascular Sciences, Amsterdam UMC, University of Amsterdam, Amsterdam, the Netherlands. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22101474067%22">Clinical and translational science</searchLink> [Clin Transl Sci] 2025 Nov; Vol. 18 (11), pp. e70388. – Name: TypePub Label: Publication Type Group: TypPub Data: Clinical Trial, Phase III; Journal Article; Multicenter Study; Randomized Controlled Trial – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22WileyBlackwell+Pub%22">WileyBlackwell Pub </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101474067 <i>Publication Model: </i>Print <i>Cited Medium: </i>Internet <i>ISSN: </i>1752-8062 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2217528054%22">17528054 </searchLink><i>NLM ISO Abbreviation: </i>Clin Transl Sci <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=41208217 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1111/cts.70388 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: e70388 Titles: – TitleFull: Exposure-Response Analysis of Donidalorsen for the Treatment of Hereditary Angioedema. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Singh P – PersonEntity: Name: NameFull: Witjes H – PersonEntity: Name: NameFull: Kleijn HJ – PersonEntity: Name: NameFull: Diep JK – PersonEntity: Name: NameFull: Bordone L – PersonEntity: Name: NameFull: Newman KB – PersonEntity: Name: NameFull: Gao X – PersonEntity: Name: NameFull: Cohn DM IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 11 Text: 2025 Nov Type: published Y: 2025 Identifiers: – Type: issn-electronic Value: 1752-8062 Numbering: – Type: volume Value: 18 – Type: issue Value: 11 Titles: – TitleFull: Clinical and translational science Type: main |
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