Cyclase-associated protein 2 gene delivery: A potential multi-target approach for preventing synaptic failure in Alzheimer's disease.

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Title: Cyclase-associated protein 2 gene delivery: A potential multi-target approach for preventing synaptic failure in Alzheimer's disease.
Authors: Stringhi R; Department of Pharmacological and Biomolecular Sciences 'Rodolfo Paoletti,' Università degli Studi di Milano, Via Giuseppe Balzaretti 9, 20133 Milan, Italy., Pelucchi S; Department of Pharmacological and Biomolecular Sciences 'Rodolfo Paoletti,' Università degli Studi di Milano, Via Giuseppe Balzaretti 9, 20133 Milan, Italy., D'Andrea L; Department of Pharmacological and Biomolecular Sciences 'Rodolfo Paoletti,' Università degli Studi di Milano, Via Giuseppe Balzaretti 9, 20133 Milan, Italy., La Greca F; Department of Pharmacological and Biomolecular Sciences 'Rodolfo Paoletti,' Università degli Studi di Milano, Via Giuseppe Balzaretti 9, 20133 Milan, Italy., Zianni E; Department of Pharmacological and Biomolecular Sciences 'Rodolfo Paoletti,' Università degli Studi di Milano, Via Giuseppe Balzaretti 9, 20133 Milan, Italy., Targa L; Department of Pharmacological and Biomolecular Sciences 'Rodolfo Paoletti,' Università degli Studi di Milano, Via Giuseppe Balzaretti 9, 20133 Milan, Italy., Mosconi C; Department of Pharmacological and Biomolecular Sciences 'Rodolfo Paoletti,' Università degli Studi di Milano, Via Giuseppe Balzaretti 9, 20133 Milan, Italy., Vandermeulen L; Department of Pharmacological and Biomolecular Sciences 'Rodolfo Paoletti,' Università degli Studi di Milano, Via Giuseppe Balzaretti 9, 20133 Milan, Italy., Ascagni M; Unitech NOLIMITS, Università degli Studi di Milano, Via Golgi 19, 20133 Milan, Italy., Speciani MC; Department of Clinical Sciences and Community Health - Dipartimento di Eccellenza 2023-2027, Branch of Medical Statistics, Biometry and Epidemiology 'G. A. Maccacaro,' Università degli Studi di Milano, Via Celoria 22, 20133 Milan, Italy., Gardoni F; Department of Pharmacological and Biomolecular Sciences 'Rodolfo Paoletti,' Università degli Studi di Milano, Via Giuseppe Balzaretti 9, 20133 Milan, Italy., Scheggia D; Department of Pharmacological and Biomolecular Sciences 'Rodolfo Paoletti,' Università degli Studi di Milano, Via Giuseppe Balzaretti 9, 20133 Milan, Italy., Edefonti V; Department of Clinical Sciences and Community Health - Dipartimento di Eccellenza 2023-2027, Branch of Medical Statistics, Biometry and Epidemiology 'G. A. Maccacaro,' Università degli Studi di Milano, Via Celoria 22, 20133 Milan, Italy; Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Via Sforza 35, 20122 Milan, Italy., Di Luca M; Department of Pharmacological and Biomolecular Sciences 'Rodolfo Paoletti,' Università degli Studi di Milano, Via Giuseppe Balzaretti 9, 20133 Milan, Italy., Marcello E; Department of Pharmacological and Biomolecular Sciences 'Rodolfo Paoletti,' Università degli Studi di Milano, Via Giuseppe Balzaretti 9, 20133 Milan, Italy. Electronic address: elena.marcello@unimi.it.
Source: Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2026 Mar 04; Vol. 34 (3), pp. 1684-1706. Date of Electronic Publication: 2025 Dec 11.
Publication Type: Journal Article
Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1525-0024
DOI:10.1016/j.ymthe.2025.12.023