| Authors: |
Pini V; Dubowitz Neuromuscular Centre - UCL Great Ormond Street Institute of Child Health, London, UK. v.pini@ucl.ac.uk.; Neuromuscular Repair Unit, Institute of Experimental Neurology, IRCCS Ospedale San Raffaele, Milan, Italy. v.pini@ucl.ac.uk., Catapano F; Dubowitz Neuromuscular Centre - UCL Great Ormond Street Institute of Child Health, London, UK., Bonaccorso R; Neuromuscular Repair Unit, Institute of Experimental Neurology, IRCCS Ospedale San Raffaele, Milan, Italy., Weisburd B; Program in Medical and Population Genetics, Broad Center for Mendelian Genomics, Broad Institute of MIT and Harvard, Cambridge, MA, USA., Previtali SC; Neuromuscular Repair Unit, Institute of Experimental Neurology, IRCCS Ospedale San Raffaele, Milan, Italy.; Vita-Salute San Raffaele University, Milan, Italy., Muntoni F; Dubowitz Neuromuscular Centre - UCL Great Ormond Street Institute of Child Health, London, UK.; NIHR Great Ormond Street Hospital Biomedical Research Centre, London, UK. |