Precision medicine with pioneering RNAi therapeutics in ATTR amyloidosis: from bench to bedside.

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Bibliographic Details
Title: Precision medicine with pioneering RNAi therapeutics in ATTR amyloidosis: from bench to bedside.
Authors: Malinverni S; Department of Molecular Medicine, Institute of Biochemistry, University of Pavia, Pavia, Italy., Vergaro G; Institute of Life Sciences, Scuola Superiore Sant'Anna, Pisa, Italy; Cardiology Division, Fondazione Toscana Gabriele Monasterio, Pisa, Italy., Verona G; National Amyloidosis Centre, Division of Medicine, University College London, Royal Free Campus Rowland Hill Street, London NW3 2PF, UK. Electronic address: g.verona@ucl.ac.uk., Porcari A; National Amyloidosis Centre, Division of Medicine, University College London, Royal Free Campus Rowland Hill Street, London NW3 2PF, UK; Centre for Diagnosis and Treatment of Cardiomyopathies, Cardiovascular Department, Azienda Sanitaria Universitaria Giuliano-Isontina (ASUGI), University of Trieste, Trieste 34149, Italy; European Reference Network for rare, low prevalence and complex diseases of the heart (ERN GUARD-Heart), Trieste, Italy.
Source: European journal of internal medicine [Eur J Intern Med] 2026 Jun; Vol. 148, pp. 106738. Date of Electronic Publication: 2026 Feb 02.
Publication Type: Journal Article; Review
Journal Info: Publisher: Elsevier Science Country of Publication: Netherlands NLM ID: 9003220 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1879-0828 (Electronic) Linking ISSN: 09536205 NLM ISO Abbreviation: Eur J Intern Med Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1879-0828
DOI:10.1016/j.ejim.2026.106738