Precision medicine with pioneering RNAi therapeutics in ATTR amyloidosis: from bench to bedside.

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Title: Precision medicine with pioneering RNAi therapeutics in ATTR amyloidosis: from bench to bedside.
Authors: Malinverni S; Department of Molecular Medicine, Institute of Biochemistry, University of Pavia, Pavia, Italy., Vergaro G; Institute of Life Sciences, Scuola Superiore Sant'Anna, Pisa, Italy; Cardiology Division, Fondazione Toscana Gabriele Monasterio, Pisa, Italy., Verona G; National Amyloidosis Centre, Division of Medicine, University College London, Royal Free Campus Rowland Hill Street, London NW3 2PF, UK. Electronic address: g.verona@ucl.ac.uk., Porcari A; National Amyloidosis Centre, Division of Medicine, University College London, Royal Free Campus Rowland Hill Street, London NW3 2PF, UK; Centre for Diagnosis and Treatment of Cardiomyopathies, Cardiovascular Department, Azienda Sanitaria Universitaria Giuliano-Isontina (ASUGI), University of Trieste, Trieste 34149, Italy; European Reference Network for rare, low prevalence and complex diseases of the heart (ERN GUARD-Heart), Trieste, Italy.
Source: European journal of internal medicine [Eur J Intern Med] 2026 Jun; Vol. 148, pp. 106738. Date of Electronic Publication: 2026 Feb 02.
Publication Type: Journal Article; Review
Journal Info: Publisher: Elsevier Science Country of Publication: Netherlands NLM ID: 9003220 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1879-0828 (Electronic) Linking ISSN: 09536205 NLM ISO Abbreviation: Eur J Intern Med Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Precision medicine with pioneering RNAi therapeutics in ATTR amyloidosis: from bench to bedside.
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  Data: <searchLink fieldCode="AU" term="%22Malinverni+S%22">Malinverni S</searchLink>; Department of Molecular Medicine, Institute of Biochemistry, University of Pavia, Pavia, Italy.<br /><searchLink fieldCode="AU" term="%22Vergaro+G%22">Vergaro G</searchLink>; Institute of Life Sciences, Scuola Superiore Sant'Anna, Pisa, Italy; Cardiology Division, Fondazione Toscana Gabriele Monasterio, Pisa, Italy.<br /><searchLink fieldCode="AU" term="%22Verona+G%22">Verona G</searchLink>; National Amyloidosis Centre, Division of Medicine, University College London, Royal Free Campus Rowland Hill Street, London NW3 2PF, UK. Electronic address: g.verona@ucl.ac.uk.<br /><searchLink fieldCode="AU" term="%22Porcari+A%22">Porcari A</searchLink>; National Amyloidosis Centre, Division of Medicine, University College London, Royal Free Campus Rowland Hill Street, London NW3 2PF, UK; Centre for Diagnosis and Treatment of Cardiomyopathies, Cardiovascular Department, Azienda Sanitaria Universitaria Giuliano-Isontina (ASUGI), University of Trieste, Trieste 34149, Italy; European Reference Network for rare, low prevalence and complex diseases of the heart (ERN GUARD-Heart), Trieste, Italy.
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  Data: <searchLink fieldCode="JN" term="%229003220%22">European journal of internal medicine</searchLink> [Eur J Intern Med] 2026 Jun; Vol. 148, pp. 106738. <i>Date of Electronic Publication: </i>2026 Feb 02.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Elsevier+Science%22">Elsevier Science </searchLink><i>Country of Publication: </i>Netherlands <i>NLM ID: </i>9003220 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1879-0828 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2209536205%22">09536205 </searchLink><i>NLM ISO Abbreviation: </i>Eur J Intern Med <i>Subsets: </i>MEDLINE
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      – Type: doi
        Value: 10.1016/j.ejim.2026.106738
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      – Code: eng
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      – TitleFull: Precision medicine with pioneering RNAi therapeutics in ATTR amyloidosis: from bench to bedside.
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              Text: 2026 Jun
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              Y: 2026
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