NXTAGE: a phase 1/2 study of NXT007 to assess safety, pharmacokinetics, and efficacy in hemophilia A without inhibitors.

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Bibliographic Details
Title: NXTAGE: a phase 1/2 study of NXT007 to assess safety, pharmacokinetics, and efficacy in hemophilia A without inhibitors.
Authors: Nogami K; Department of Pediatrics, Nara Medical University, Nara, Japan., You CW; Department of Pediatrics, Daejeon Eulji Medical Center, Eulji University School of Medicine, Daejeon, Republic of Korea., Park YS; Department of Pediatrics, Kyung Hee University Hospital at Gangdong, Seoul, Republic of Korea., Chen YC; Hemophilia Care and Research Center, Tri-Service General Hospital, Taipei, Taiwan., Shen MC; Department of Internal Medicine, Changhua Christian Hospital, Changhua, Taiwan., Wang JD; Center for Rare Disease and Hemophilia, Taichung Veterans General Hospital, Taichung, Taiwan., Takeyama M; Division of Hemophilia, National Hospital Organization, Osaka National Hospital, Osaka, Japan., Amano K; Department of Laboratory Medicine, Tokyo Medical University, Tokyo, Japan., Chou SC; Department of Internal Medicine, National Taiwan University Hospital, Taipei, Taiwan., Miwa T; Chugai Pharmaceutical Co, Ltd, Tokyo, Japan., Chen CA; Chugai Pharmaceutical Co, Ltd, Tokyo, Japan., Miyake T; Chugai Pharmaceutical Co, Ltd, Tokyo, Japan., Iwasaki K; Chugai Pharmaceutical Co, Ltd, Tokyo, Japan., Kobayashi R; Chugai Pharmaceutical Co, Ltd, Tokyo, Japan., Shima M; Department of Pediatrics, Nara Medical University, Nara, Japan.; Thrombosis and Hemostasis Research Center, Nara Medical University, Nara, Japan.
Source: Blood [Blood] 2026 May 07; Vol. 147 (19), pp. 2261-2271.
Publication Type: Journal Article; Clinical Trial, Phase I; Clinical Trial, Phase II; Multicenter Study
Journal Info: Publisher: Elsevier Country of Publication: United States NLM ID: 7603509 Publication Model: Print Cited Medium: Internet ISSN: 1528-0020 (Electronic) Linking ISSN: 00064971 NLM ISO Abbreviation: Blood Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1528-0020
DOI:10.1182/blood.2025031894