An Antibody-Oligonucleotide Conjugate for Myotonic Dystrophy Type 1.

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Bibliographic Details
Title: An Antibody-Oligonucleotide Conjugate for Myotonic Dystrophy Type 1.
Authors: Johnson NE; Virginia Commonwealth University, Richmond., Tai LJ; Avidity Biosciences, San Diego, CA., Hamel JI; University of Rochester Medical Center, Rochester, NY., Day JW; Stanford University Medical Center, Palo Alto, CA., Statland JM; University of Kansas Medical Center, Kansas City., Soltanzadeh P; University of California, Los Angeles, Los Angeles., Subramony SH; University of Florida, Gainesville., Thornton CA; University of Rochester Medical Center, Rochester, NY., Arnold WD; University of Missouri, Columbia., Wicklund M; University of Texas, San Antonio., Freimer ML; Ohio State University, Columbus., Eichinger K; University of Rochester Medical Center, Rochester, NY., Dekdebrun J; University of Rochester Medical Center, Rochester, NY., Chen CY; Avidity Biosciences, San Diego, CA., Goel V; Avidity Biosciences, San Diego, CA., McEvoy B; Avidity Biosciences, San Diego, CA., Zhu Y; Avidity Biosciences, San Diego, CA., Hughes SG; Avidity Biosciences, San Diego, CA., Ackermann EJ; Avidity Biosciences, San Diego, CA., Levin AA; Avidity Biosciences, San Diego, CA.
Source: The New England journal of medicine [N Engl J Med] 2026 Feb 19; Vol. 394 (8), pp. 763-772.
Publication Type: Journal Article; Randomized Controlled Trial; Multicenter Study; Clinical Trial, Phase II; Clinical Trial, Phase I
Journal Info: Publisher: Massachusetts Medical Society Country of Publication: United States NLM ID: 0255562 Publication Model: Print Cited Medium: Internet ISSN: 1533-4406 (Electronic) Linking ISSN: 00284793 NLM ISO Abbreviation: N Engl J Med Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1533-4406
DOI:10.1056/NEJMoa2407326