An Antibody-Oligonucleotide Conjugate for Myotonic Dystrophy Type 1.
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| Title: | An Antibody-Oligonucleotide Conjugate for Myotonic Dystrophy Type 1. |
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| Authors: | Johnson NE; Virginia Commonwealth University, Richmond., Tai LJ; Avidity Biosciences, San Diego, CA., Hamel JI; University of Rochester Medical Center, Rochester, NY., Day JW; Stanford University Medical Center, Palo Alto, CA., Statland JM; University of Kansas Medical Center, Kansas City., Soltanzadeh P; University of California, Los Angeles, Los Angeles., Subramony SH; University of Florida, Gainesville., Thornton CA; University of Rochester Medical Center, Rochester, NY., Arnold WD; University of Missouri, Columbia., Wicklund M; University of Texas, San Antonio., Freimer ML; Ohio State University, Columbus., Eichinger K; University of Rochester Medical Center, Rochester, NY., Dekdebrun J; University of Rochester Medical Center, Rochester, NY., Chen CY; Avidity Biosciences, San Diego, CA., Goel V; Avidity Biosciences, San Diego, CA., McEvoy B; Avidity Biosciences, San Diego, CA., Zhu Y; Avidity Biosciences, San Diego, CA., Hughes SG; Avidity Biosciences, San Diego, CA., Ackermann EJ; Avidity Biosciences, San Diego, CA., Levin AA; Avidity Biosciences, San Diego, CA. |
| Source: | The New England journal of medicine [N Engl J Med] 2026 Feb 19; Vol. 394 (8), pp. 763-772. |
| Publication Type: | Journal Article; Randomized Controlled Trial; Multicenter Study; Clinical Trial, Phase II; Clinical Trial, Phase I |
| Journal Info: | Publisher: Massachusetts Medical Society Country of Publication: United States NLM ID: 0255562 Publication Model: Print Cited Medium: Internet ISSN: 1533-4406 (Electronic) Linking ISSN: 00284793 NLM ISO Abbreviation: N Engl J Med Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 41707138 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: An Antibody-Oligonucleotide Conjugate for Myotonic Dystrophy Type 1. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Johnson+NE%22">Johnson NE</searchLink>; Virginia Commonwealth University, Richmond.<br /><searchLink fieldCode="AU" term="%22Tai+LJ%22">Tai LJ</searchLink>; Avidity Biosciences, San Diego, CA.<br /><searchLink fieldCode="AU" term="%22Hamel+JI%22">Hamel JI</searchLink>; University of Rochester Medical Center, Rochester, NY.<br /><searchLink fieldCode="AU" term="%22Day+JW%22">Day JW</searchLink>; Stanford University Medical Center, Palo Alto, CA.<br /><searchLink fieldCode="AU" term="%22Statland+JM%22">Statland JM</searchLink>; University of Kansas Medical Center, Kansas City.<br /><searchLink fieldCode="AU" term="%22Soltanzadeh+P%22">Soltanzadeh P</searchLink>; University of California, Los Angeles, Los Angeles.<br /><searchLink fieldCode="AU" term="%22Subramony+SH%22">Subramony SH</searchLink>; University of Florida, Gainesville.<br /><searchLink fieldCode="AU" term="%22Thornton+CA%22">Thornton CA</searchLink>; University of Rochester Medical Center, Rochester, NY.<br /><searchLink fieldCode="AU" term="%22Arnold+WD%22">Arnold WD</searchLink>; University of Missouri, Columbia.<br /><searchLink fieldCode="AU" term="%22Wicklund+M%22">Wicklund M</searchLink>; University of Texas, San Antonio.<br /><searchLink fieldCode="AU" term="%22Freimer+ML%22">Freimer ML</searchLink>; Ohio State University, Columbus.<br /><searchLink fieldCode="AU" term="%22Eichinger+K%22">Eichinger K</searchLink>; University of Rochester Medical Center, Rochester, NY.<br /><searchLink fieldCode="AU" term="%22Dekdebrun+J%22">Dekdebrun J</searchLink>; University of Rochester Medical Center, Rochester, NY.<br /><searchLink fieldCode="AU" term="%22Chen+CY%22">Chen CY</searchLink>; Avidity Biosciences, San Diego, CA.<br /><searchLink fieldCode="AU" term="%22Goel+V%22">Goel V</searchLink>; Avidity Biosciences, San Diego, CA.<br /><searchLink fieldCode="AU" term="%22McEvoy+B%22">McEvoy B</searchLink>; Avidity Biosciences, San Diego, CA.<br /><searchLink fieldCode="AU" term="%22Zhu+Y%22">Zhu Y</searchLink>; Avidity Biosciences, San Diego, CA.<br /><searchLink fieldCode="AU" term="%22Hughes+SG%22">Hughes SG</searchLink>; Avidity Biosciences, San Diego, CA.<br /><searchLink fieldCode="AU" term="%22Ackermann+EJ%22">Ackermann EJ</searchLink>; Avidity Biosciences, San Diego, CA.<br /><searchLink fieldCode="AU" term="%22Levin+AA%22">Levin AA</searchLink>; Avidity Biosciences, San Diego, CA. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%220255562%22">The New England journal of medicine</searchLink> [N Engl J Med] 2026 Feb 19; Vol. 394 (8), pp. 763-772. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article; Randomized Controlled Trial; Multicenter Study; Clinical Trial, Phase II; Clinical Trial, Phase I – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Massachusetts+Medical+Society%22">Massachusetts Medical Society </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>0255562 <i>Publication Model: </i>Print <i>Cited Medium: </i>Internet <i>ISSN: </i>1533-4406 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2200284793%22">00284793 </searchLink><i>NLM ISO Abbreviation: </i>N Engl J Med <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=41707138 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1056/NEJMoa2407326 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: 763 Titles: – TitleFull: An Antibody-Oligonucleotide Conjugate for Myotonic Dystrophy Type 1. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Johnson NE – PersonEntity: Name: NameFull: Tai LJ – PersonEntity: Name: NameFull: Hamel JI – PersonEntity: Name: NameFull: Day JW – PersonEntity: Name: NameFull: Statland JM – PersonEntity: Name: NameFull: Soltanzadeh P – PersonEntity: Name: NameFull: Subramony SH – PersonEntity: Name: NameFull: Thornton CA – PersonEntity: Name: NameFull: Arnold WD – PersonEntity: Name: NameFull: Wicklund M – PersonEntity: Name: NameFull: Freimer ML – PersonEntity: Name: NameFull: Eichinger K – PersonEntity: Name: NameFull: Dekdebrun J – PersonEntity: Name: NameFull: Chen CY – PersonEntity: Name: NameFull: Goel V – PersonEntity: Name: NameFull: McEvoy B – PersonEntity: Name: NameFull: Zhu Y – PersonEntity: Name: NameFull: Hughes SG – PersonEntity: Name: NameFull: Ackermann EJ – PersonEntity: Name: NameFull: Levin AA IsPartOfRelationships: – BibEntity: Dates: – D: 19 M: 02 Text: 2026 Feb 19 Type: published Y: 2026 Identifiers: – Type: issn-electronic Value: 1533-4406 Numbering: – Type: volume Value: 394 – Type: issue Value: 8 Titles: – TitleFull: The New England journal of medicine Type: main |
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