An Antibody-Oligonucleotide Conjugate for Myotonic Dystrophy Type 1.

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Title: An Antibody-Oligonucleotide Conjugate for Myotonic Dystrophy Type 1.
Authors: Johnson NE; Virginia Commonwealth University, Richmond., Tai LJ; Avidity Biosciences, San Diego, CA., Hamel JI; University of Rochester Medical Center, Rochester, NY., Day JW; Stanford University Medical Center, Palo Alto, CA., Statland JM; University of Kansas Medical Center, Kansas City., Soltanzadeh P; University of California, Los Angeles, Los Angeles., Subramony SH; University of Florida, Gainesville., Thornton CA; University of Rochester Medical Center, Rochester, NY., Arnold WD; University of Missouri, Columbia., Wicklund M; University of Texas, San Antonio., Freimer ML; Ohio State University, Columbus., Eichinger K; University of Rochester Medical Center, Rochester, NY., Dekdebrun J; University of Rochester Medical Center, Rochester, NY., Chen CY; Avidity Biosciences, San Diego, CA., Goel V; Avidity Biosciences, San Diego, CA., McEvoy B; Avidity Biosciences, San Diego, CA., Zhu Y; Avidity Biosciences, San Diego, CA., Hughes SG; Avidity Biosciences, San Diego, CA., Ackermann EJ; Avidity Biosciences, San Diego, CA., Levin AA; Avidity Biosciences, San Diego, CA.
Source: The New England journal of medicine [N Engl J Med] 2026 Feb 19; Vol. 394 (8), pp. 763-772.
Publication Type: Journal Article; Randomized Controlled Trial; Multicenter Study; Clinical Trial, Phase II; Clinical Trial, Phase I
Journal Info: Publisher: Massachusetts Medical Society Country of Publication: United States NLM ID: 0255562 Publication Model: Print Cited Medium: Internet ISSN: 1533-4406 (Electronic) Linking ISSN: 00284793 NLM ISO Abbreviation: N Engl J Med Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: An Antibody-Oligonucleotide Conjugate for Myotonic Dystrophy Type 1.
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  Data: <searchLink fieldCode="AU" term="%22Johnson+NE%22">Johnson NE</searchLink>; Virginia Commonwealth University, Richmond.<br /><searchLink fieldCode="AU" term="%22Tai+LJ%22">Tai LJ</searchLink>; Avidity Biosciences, San Diego, CA.<br /><searchLink fieldCode="AU" term="%22Hamel+JI%22">Hamel JI</searchLink>; University of Rochester Medical Center, Rochester, NY.<br /><searchLink fieldCode="AU" term="%22Day+JW%22">Day JW</searchLink>; Stanford University Medical Center, Palo Alto, CA.<br /><searchLink fieldCode="AU" term="%22Statland+JM%22">Statland JM</searchLink>; University of Kansas Medical Center, Kansas City.<br /><searchLink fieldCode="AU" term="%22Soltanzadeh+P%22">Soltanzadeh P</searchLink>; University of California, Los Angeles, Los Angeles.<br /><searchLink fieldCode="AU" term="%22Subramony+SH%22">Subramony SH</searchLink>; University of Florida, Gainesville.<br /><searchLink fieldCode="AU" term="%22Thornton+CA%22">Thornton CA</searchLink>; University of Rochester Medical Center, Rochester, NY.<br /><searchLink fieldCode="AU" term="%22Arnold+WD%22">Arnold WD</searchLink>; University of Missouri, Columbia.<br /><searchLink fieldCode="AU" term="%22Wicklund+M%22">Wicklund M</searchLink>; University of Texas, San Antonio.<br /><searchLink fieldCode="AU" term="%22Freimer+ML%22">Freimer ML</searchLink>; Ohio State University, Columbus.<br /><searchLink fieldCode="AU" term="%22Eichinger+K%22">Eichinger K</searchLink>; University of Rochester Medical Center, Rochester, NY.<br /><searchLink fieldCode="AU" term="%22Dekdebrun+J%22">Dekdebrun J</searchLink>; University of Rochester Medical Center, Rochester, NY.<br /><searchLink fieldCode="AU" term="%22Chen+CY%22">Chen CY</searchLink>; Avidity Biosciences, San Diego, CA.<br /><searchLink fieldCode="AU" term="%22Goel+V%22">Goel V</searchLink>; Avidity Biosciences, San Diego, CA.<br /><searchLink fieldCode="AU" term="%22McEvoy+B%22">McEvoy B</searchLink>; Avidity Biosciences, San Diego, CA.<br /><searchLink fieldCode="AU" term="%22Zhu+Y%22">Zhu Y</searchLink>; Avidity Biosciences, San Diego, CA.<br /><searchLink fieldCode="AU" term="%22Hughes+SG%22">Hughes SG</searchLink>; Avidity Biosciences, San Diego, CA.<br /><searchLink fieldCode="AU" term="%22Ackermann+EJ%22">Ackermann EJ</searchLink>; Avidity Biosciences, San Diego, CA.<br /><searchLink fieldCode="AU" term="%22Levin+AA%22">Levin AA</searchLink>; Avidity Biosciences, San Diego, CA.
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  Data: <searchLink fieldCode="JN" term="%220255562%22">The New England journal of medicine</searchLink> [N Engl J Med] 2026 Feb 19; Vol. 394 (8), pp. 763-772.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Massachusetts+Medical+Society%22">Massachusetts Medical Society </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>0255562 <i>Publication Model: </i>Print <i>Cited Medium: </i>Internet <i>ISSN: </i>1533-4406 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2200284793%22">00284793 </searchLink><i>NLM ISO Abbreviation: </i>N Engl J Med <i>Subsets: </i>MEDLINE
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              Text: 2026 Feb 19
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