Impact of RNAi therapeutics on cardiac parameters in patients with hereditary transthyretin amyloidosis initially treated with stabilizers: A French real-world study.

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Title: Impact of RNAi therapeutics on cardiac parameters in patients with hereditary transthyretin amyloidosis initially treated with stabilizers: A French real-world study.
Authors: Fraix A; Cardiology Department, CHRU Nancy, Site Brabois, 54500 Vandœuvre, France., Algalarrondo V; Referral centre for cardiac amyloidosis CERAMIC-Cardio, Cardiology Department, Bichat Hospital, AP-HP, 75018 Paris, France., Lairez O; Department of Cardiology, CHU de Toulouse, 31400 Toulouse, France; Department of Nuclear Medicine, CHU de Toulouse, 31400 Toulouse, France; Cardiac Imaging Centre, Medical School, CHU de Toulouse, Toulouse III Paul Sabatier University, 31400 Toulouse, France., Arnal M; Department of Cardiology, Bichat University Hospital, AP-HP, 75018 Paris, France., Piriou N; Inserm, Reference Centre for cardiomyopathies, CIC 1413, Thorax Institute, CHU de Nantes, Nantes University, 44000 Nantes, France., Michaud M; Cardiology Department, CHRU Nancy, Site Brabois, 54500 Vandœuvre, France., Habib G; Cardiology Department, La Timone Hospital, AP-HM, 264, 13005 Marseille, France., Roubille F; Inserm, PhyMedExp, CNRS, Cardiology Department, CHU de Montpellier, Montpellier University, 34000 Montpellier, France., Lucas C; Cardiology Department, La Timone Hospital, AP-HM, 264, 13005 Marseille, France., Duval AJ; Inserm 1060 & 1407, Heart Failure Department, Clinical Investigation Centre, Civil Hospices of Lyon, University Claude-Bernard Lyon 1, 69000 Lyon, France., Bachelet B; Department of Cardiology, CHU de Toulouse, 31400 Toulouse, France; Cardiac Imaging Centre, Medical School, CHU de Toulouse, Toulouse III Paul Sabatier University, 31400 Toulouse, France., Donal E; Inserm 1099, Department of Cardiology, LTSI, LTSI, CHU de Rennes, University of Rennes, 35000 Rennes, France., Damy T; Inserm U955, IMRB, Department of Cardiology and French Referral Centre for Cardiac Amyloidosis, East Paris Creteil University, Henri-Mondor Hospital, AP-HP, 94000 Créteil, France., Réant P; CIC-P 1401, University Hospital Centre of Bordeaux, Bordeaux University, 33000 Bordeaux, France., Kharoubi M; Inserm U955, IMRB, Department of Cardiology and French Referral Centre for Cardiac Amyloidosis, East Paris Creteil University, Henri-Mondor Hospital, AP-HP, 94000 Créteil, France., Huttin O; Cardiology Department, CHRU Nancy, Site Brabois, 54500 Vandœuvre, France. Electronic address: drhuttinolivier@gmail.com.
Source: Archives of cardiovascular diseases [Arch Cardiovasc Dis] 2026 Jun-Jul; Vol. 119 (6-7), pp. 452-460. Date of Electronic Publication: 2026 Feb 09.
Publication Type: Journal Article; Multicenter Study; Observational Study
Journal Info: Publisher: Elsevier Masson Country of Publication: Netherlands NLM ID: 101465655 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1875-2128 (Electronic) Linking ISSN: 18752128 NLM ISO Abbreviation: Arch Cardiovasc Dis Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1875-2128
DOI:10.1016/j.acvd.2025.11.014