Impact of RNAi therapeutics on cardiac parameters in patients with hereditary transthyretin amyloidosis initially treated with stabilizers: A French real-world study.

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Title: Impact of RNAi therapeutics on cardiac parameters in patients with hereditary transthyretin amyloidosis initially treated with stabilizers: A French real-world study.
Authors: Fraix A; Cardiology Department, CHRU Nancy, Site Brabois, 54500 Vandœuvre, France., Algalarrondo V; Referral centre for cardiac amyloidosis CERAMIC-Cardio, Cardiology Department, Bichat Hospital, AP-HP, 75018 Paris, France., Lairez O; Department of Cardiology, CHU de Toulouse, 31400 Toulouse, France; Department of Nuclear Medicine, CHU de Toulouse, 31400 Toulouse, France; Cardiac Imaging Centre, Medical School, CHU de Toulouse, Toulouse III Paul Sabatier University, 31400 Toulouse, France., Arnal M; Department of Cardiology, Bichat University Hospital, AP-HP, 75018 Paris, France., Piriou N; Inserm, Reference Centre for cardiomyopathies, CIC 1413, Thorax Institute, CHU de Nantes, Nantes University, 44000 Nantes, France., Michaud M; Cardiology Department, CHRU Nancy, Site Brabois, 54500 Vandœuvre, France., Habib G; Cardiology Department, La Timone Hospital, AP-HM, 264, 13005 Marseille, France., Roubille F; Inserm, PhyMedExp, CNRS, Cardiology Department, CHU de Montpellier, Montpellier University, 34000 Montpellier, France., Lucas C; Cardiology Department, La Timone Hospital, AP-HM, 264, 13005 Marseille, France., Duval AJ; Inserm 1060 & 1407, Heart Failure Department, Clinical Investigation Centre, Civil Hospices of Lyon, University Claude-Bernard Lyon 1, 69000 Lyon, France., Bachelet B; Department of Cardiology, CHU de Toulouse, 31400 Toulouse, France; Cardiac Imaging Centre, Medical School, CHU de Toulouse, Toulouse III Paul Sabatier University, 31400 Toulouse, France., Donal E; Inserm 1099, Department of Cardiology, LTSI, LTSI, CHU de Rennes, University of Rennes, 35000 Rennes, France., Damy T; Inserm U955, IMRB, Department of Cardiology and French Referral Centre for Cardiac Amyloidosis, East Paris Creteil University, Henri-Mondor Hospital, AP-HP, 94000 Créteil, France., Réant P; CIC-P 1401, University Hospital Centre of Bordeaux, Bordeaux University, 33000 Bordeaux, France., Kharoubi M; Inserm U955, IMRB, Department of Cardiology and French Referral Centre for Cardiac Amyloidosis, East Paris Creteil University, Henri-Mondor Hospital, AP-HP, 94000 Créteil, France., Huttin O; Cardiology Department, CHRU Nancy, Site Brabois, 54500 Vandœuvre, France. Electronic address: drhuttinolivier@gmail.com.
Source: Archives of cardiovascular diseases [Arch Cardiovasc Dis] 2026 Jun-Jul; Vol. 119 (6-7), pp. 452-460. Date of Electronic Publication: 2026 Feb 09.
Publication Type: Journal Article; Multicenter Study; Observational Study
Journal Info: Publisher: Elsevier Masson Country of Publication: Netherlands NLM ID: 101465655 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1875-2128 (Electronic) Linking ISSN: 18752128 NLM ISO Abbreviation: Arch Cardiovasc Dis Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Impact of RNAi therapeutics on cardiac parameters in patients with hereditary transthyretin amyloidosis initially treated with stabilizers: A French real-world study.
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  Data: <searchLink fieldCode="AU" term="%22Fraix+A%22">Fraix A</searchLink>; Cardiology Department, CHRU Nancy, Site Brabois, 54500 Vandœuvre, France.<br /><searchLink fieldCode="AU" term="%22Algalarrondo+V%22">Algalarrondo V</searchLink>; Referral centre for cardiac amyloidosis CERAMIC-Cardio, Cardiology Department, Bichat Hospital, AP-HP, 75018 Paris, France.<br /><searchLink fieldCode="AU" term="%22Lairez+O%22">Lairez O</searchLink>; Department of Cardiology, CHU de Toulouse, 31400 Toulouse, France; Department of Nuclear Medicine, CHU de Toulouse, 31400 Toulouse, France; Cardiac Imaging Centre, Medical School, CHU de Toulouse, Toulouse III Paul Sabatier University, 31400 Toulouse, France.<br /><searchLink fieldCode="AU" term="%22Arnal+M%22">Arnal M</searchLink>; Department of Cardiology, Bichat University Hospital, AP-HP, 75018 Paris, France.<br /><searchLink fieldCode="AU" term="%22Piriou+N%22">Piriou N</searchLink>; Inserm, Reference Centre for cardiomyopathies, CIC 1413, Thorax Institute, CHU de Nantes, Nantes University, 44000 Nantes, France.<br /><searchLink fieldCode="AU" term="%22Michaud+M%22">Michaud M</searchLink>; Cardiology Department, CHRU Nancy, Site Brabois, 54500 Vandœuvre, France.<br /><searchLink fieldCode="AU" term="%22Habib+G%22">Habib G</searchLink>; Cardiology Department, La Timone Hospital, AP-HM, 264, 13005 Marseille, France.<br /><searchLink fieldCode="AU" term="%22Roubille+F%22">Roubille F</searchLink>; Inserm, PhyMedExp, CNRS, Cardiology Department, CHU de Montpellier, Montpellier University, 34000 Montpellier, France.<br /><searchLink fieldCode="AU" term="%22Lucas+C%22">Lucas C</searchLink>; Cardiology Department, La Timone Hospital, AP-HM, 264, 13005 Marseille, France.<br /><searchLink fieldCode="AU" term="%22Duval+AJ%22">Duval AJ</searchLink>; Inserm 1060 & 1407, Heart Failure Department, Clinical Investigation Centre, Civil Hospices of Lyon, University Claude-Bernard Lyon 1, 69000 Lyon, France.<br /><searchLink fieldCode="AU" term="%22Bachelet+B%22">Bachelet B</searchLink>; Department of Cardiology, CHU de Toulouse, 31400 Toulouse, France; Cardiac Imaging Centre, Medical School, CHU de Toulouse, Toulouse III Paul Sabatier University, 31400 Toulouse, France.<br /><searchLink fieldCode="AU" term="%22Donal+E%22">Donal E</searchLink>; Inserm 1099, Department of Cardiology, LTSI, LTSI, CHU de Rennes, University of Rennes, 35000 Rennes, France.<br /><searchLink fieldCode="AU" term="%22Damy+T%22">Damy T</searchLink>; Inserm U955, IMRB, Department of Cardiology and French Referral Centre for Cardiac Amyloidosis, East Paris Creteil University, Henri-Mondor Hospital, AP-HP, 94000 Créteil, France.<br /><searchLink fieldCode="AU" term="%22Réant+P%22">Réant P</searchLink>; CIC-P 1401, University Hospital Centre of Bordeaux, Bordeaux University, 33000 Bordeaux, France.<br /><searchLink fieldCode="AU" term="%22Kharoubi+M%22">Kharoubi M</searchLink>; Inserm U955, IMRB, Department of Cardiology and French Referral Centre for Cardiac Amyloidosis, East Paris Creteil University, Henri-Mondor Hospital, AP-HP, 94000 Créteil, France.<br /><searchLink fieldCode="AU" term="%22Huttin+O%22">Huttin O</searchLink>; Cardiology Department, CHRU Nancy, Site Brabois, 54500 Vandœuvre, France. Electronic address: drhuttinolivier@gmail.com.
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  Data: <searchLink fieldCode="JN" term="%22101465655%22">Archives of cardiovascular diseases</searchLink> [Arch Cardiovasc Dis] 2026 Jun-Jul; Vol. 119 (6-7), pp. 452-460. <i>Date of Electronic Publication: </i>2026 Feb 09.
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  Data: Journal Article; Multicenter Study; Observational Study
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Elsevier+Masson%22">Elsevier Masson </searchLink><i>Country of Publication: </i>Netherlands <i>NLM ID: </i>101465655 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1875-2128 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2218752128%22">18752128 </searchLink><i>NLM ISO Abbreviation: </i>Arch Cardiovasc Dis <i>Subsets: </i>MEDLINE
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        Value: 10.1016/j.acvd.2025.11.014
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        Text: English
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