| Authors: |
Irving M; Guy's and St Thomas' NHS Trust, London, UK. melitairving@nhs.net., Greco E; Women's Health Research Unit, Wolfson Institute of Population Health, Queen Mary University London, London, UK., Cocca A; Guy's and St Thomas' NHS Trust, London, UK., Dauber A; Children's National Hospital, Washington, DC, USA., Jorge AAL; Genetic Endocrinology Unit (LIM25), Endocrinology Division, Faculdade de Medicina da, Universidade de São Paulo (HC-FMUSP), São Paulo, 01246-903, Brazil., Fredwall S; National Centre for Rare Diseases, Unit Sunnaas & Oslo University Hospital Rikshospitalet, Oslo, Norway., Patterson A; Johns Hopkins University, Baltimore, MD, USA., Llerena J Jr; Instituto Nacional Fernandes Figueira, Rio de Janeiro, Brazil., Ozono K; ISEIKAI International General Hospital, Osaka, Japan., Santos R; Guy's and St Thomas' NHS Trust, London, UK., Kelly D; BridgeBio Pharma, San Francisco, CA, USA., Muslimova E; BridgeBio Pharma, San Francisco, CA, USA., Reddi T; BridgeBio Pharma, San Francisco, CA, USA., Shediac R; BridgeBio Pharma, San Francisco, CA, USA., Savarirayan R; Murdoch Children's Research Institute, Melbourne, Australia., Sutton VR; Baylor College of Medicine & Texas Children's Hospital, Houston, TX, USA., Hoover-Fong J; Johns Hopkins University, Baltimore, MD, USA., Cheung M; Great Ormond Street Hospital for Children, NHS Foundation Trust, London, UK. |