In vitro and in vivo rescue of dopaminergic neurons in Parkinson's disease models after Parkin gene therapy.
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| Title: | In vitro and in vivo rescue of dopaminergic neurons in Parkinson's disease models after Parkin gene therapy. |
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| Authors: | Hioki T; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan. takeshi.hioki@takeda.com., Nishimura M; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan., Sun X; Research, Takeda Development Center Americas Inc, Cambridge, MA, USA., Jacobo SM; Research, Takeda Development Center Americas Inc, Cambridge, MA, USA., Nakayama M; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan., Nishihara M; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan., Tohyama K; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan., Liu PT; Research, Takeda Development Center Americas Inc, Cambridge, MA, USA., Okai T; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan., Tanaka M; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan., Proetzel G; Research, Takeda Development Center Americas Inc, Cambridge, MA, USA. |
| Source: | Gene therapy [Gene Ther] 2026 Mar 05. Date of Electronic Publication: 2026 Mar 05. |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Nature Publishing Group Country of Publication: England NLM ID: 9421525 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1476-5462 (Electronic) Linking ISSN: 09697128 NLM ISO Abbreviation: Gene Ther Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 41786869 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: In vitro and in vivo rescue of dopaminergic neurons in Parkinson's disease models after Parkin gene therapy. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Hioki+T%22">Hioki T</searchLink>; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan. takeshi.hioki@takeda.com.<br /><searchLink fieldCode="AU" term="%22Nishimura+M%22">Nishimura M</searchLink>; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan.<br /><searchLink fieldCode="AU" term="%22Sun+X%22">Sun X</searchLink>; Research, Takeda Development Center Americas Inc, Cambridge, MA, USA.<br /><searchLink fieldCode="AU" term="%22Jacobo+SM%22">Jacobo SM</searchLink>; Research, Takeda Development Center Americas Inc, Cambridge, MA, USA.<br /><searchLink fieldCode="AU" term="%22Nakayama+M%22">Nakayama M</searchLink>; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan.<br /><searchLink fieldCode="AU" term="%22Nishihara+M%22">Nishihara M</searchLink>; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan.<br /><searchLink fieldCode="AU" term="%22Tohyama+K%22">Tohyama K</searchLink>; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan.<br /><searchLink fieldCode="AU" term="%22Liu+PT%22">Liu PT</searchLink>; Research, Takeda Development Center Americas Inc, Cambridge, MA, USA.<br /><searchLink fieldCode="AU" term="%22Okai+T%22">Okai T</searchLink>; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan.<br /><searchLink fieldCode="AU" term="%22Tanaka+M%22">Tanaka M</searchLink>; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan.<br /><searchLink fieldCode="AU" term="%22Proetzel+G%22">Proetzel G</searchLink>; Research, Takeda Development Center Americas Inc, Cambridge, MA, USA. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%229421525%22">Gene therapy</searchLink> [Gene Ther] 2026 Mar 05. <i>Date of Electronic Publication: </i>2026 Mar 05. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Nature+Publishing+Group%22">Nature Publishing Group </searchLink><i>Country of Publication: </i>England <i>NLM ID: </i>9421525 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1476-5462 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2209697128%22">09697128 </searchLink><i>NLM ISO Abbreviation: </i>Gene Ther <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=41786869 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1038/s41434-026-00599-0 Languages: – Code: eng Text: English Titles: – TitleFull: In vitro and in vivo rescue of dopaminergic neurons in Parkinson's disease models after Parkin gene therapy. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Hioki T – PersonEntity: Name: NameFull: Nishimura M – PersonEntity: Name: NameFull: Sun X – PersonEntity: Name: NameFull: Jacobo SM – PersonEntity: Name: NameFull: Nakayama M – PersonEntity: Name: NameFull: Nishihara M – PersonEntity: Name: NameFull: Tohyama K – PersonEntity: Name: NameFull: Liu PT – PersonEntity: Name: NameFull: Okai T – PersonEntity: Name: NameFull: Tanaka M – PersonEntity: Name: NameFull: Proetzel G IsPartOfRelationships: – BibEntity: Dates: – D: 05 M: 03 Text: 2026 Mar 05 Type: published Y: 2026 Identifiers: – Type: issn-electronic Value: 1476-5462 Titles: – TitleFull: Gene therapy Type: main |
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