In vitro and in vivo rescue of dopaminergic neurons in Parkinson's disease models after Parkin gene therapy.

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Title: In vitro and in vivo rescue of dopaminergic neurons in Parkinson's disease models after Parkin gene therapy.
Authors: Hioki T; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan. takeshi.hioki@takeda.com., Nishimura M; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan., Sun X; Research, Takeda Development Center Americas Inc, Cambridge, MA, USA., Jacobo SM; Research, Takeda Development Center Americas Inc, Cambridge, MA, USA., Nakayama M; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan., Nishihara M; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan., Tohyama K; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan., Liu PT; Research, Takeda Development Center Americas Inc, Cambridge, MA, USA., Okai T; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan., Tanaka M; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan., Proetzel G; Research, Takeda Development Center Americas Inc, Cambridge, MA, USA.
Source: Gene therapy [Gene Ther] 2026 Mar 05. Date of Electronic Publication: 2026 Mar 05.
Publication Type: Journal Article
Journal Info: Publisher: Nature Publishing Group Country of Publication: England NLM ID: 9421525 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1476-5462 (Electronic) Linking ISSN: 09697128 NLM ISO Abbreviation: Gene Ther Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: In vitro and in vivo rescue of dopaminergic neurons in Parkinson's disease models after Parkin gene therapy.
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  Data: <searchLink fieldCode="AU" term="%22Hioki+T%22">Hioki T</searchLink>; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan. takeshi.hioki@takeda.com.<br /><searchLink fieldCode="AU" term="%22Nishimura+M%22">Nishimura M</searchLink>; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan.<br /><searchLink fieldCode="AU" term="%22Sun+X%22">Sun X</searchLink>; Research, Takeda Development Center Americas Inc, Cambridge, MA, USA.<br /><searchLink fieldCode="AU" term="%22Jacobo+SM%22">Jacobo SM</searchLink>; Research, Takeda Development Center Americas Inc, Cambridge, MA, USA.<br /><searchLink fieldCode="AU" term="%22Nakayama+M%22">Nakayama M</searchLink>; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan.<br /><searchLink fieldCode="AU" term="%22Nishihara+M%22">Nishihara M</searchLink>; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan.<br /><searchLink fieldCode="AU" term="%22Tohyama+K%22">Tohyama K</searchLink>; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan.<br /><searchLink fieldCode="AU" term="%22Liu+PT%22">Liu PT</searchLink>; Research, Takeda Development Center Americas Inc, Cambridge, MA, USA.<br /><searchLink fieldCode="AU" term="%22Okai+T%22">Okai T</searchLink>; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan.<br /><searchLink fieldCode="AU" term="%22Tanaka+M%22">Tanaka M</searchLink>; Research, Takeda Pharmaceutical Company Limited, Fujisawa, Kanagawa, Japan.<br /><searchLink fieldCode="AU" term="%22Proetzel+G%22">Proetzel G</searchLink>; Research, Takeda Development Center Americas Inc, Cambridge, MA, USA.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Nature+Publishing+Group%22">Nature Publishing Group </searchLink><i>Country of Publication: </i>England <i>NLM ID: </i>9421525 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1476-5462 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2209697128%22">09697128 </searchLink><i>NLM ISO Abbreviation: </i>Gene Ther <i>Subsets: </i>MEDLINE
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        Value: 10.1038/s41434-026-00599-0
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        Text: English
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      – TitleFull: In vitro and in vivo rescue of dopaminergic neurons in Parkinson's disease models after Parkin gene therapy.
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              Text: 2026 Mar 05
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