ONC206 demonstrates potent antitumorigenic activity and is a potential novel therapeutic strategy for high-risk medulloblastoma.

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Title: ONC206 demonstrates potent antitumorigenic activity and is a potential novel therapeutic strategy for high-risk medulloblastoma.
Authors: Tzaridis T; Cancer Genome and Epigenetics Program, NCI-Designated Cancer Center, Sanford Burnham Prebys Medical Discovery Institute, La Jolla, California, USA., Liu J; Department of Pediatrics, Emory University School of Medicine, Atlanta, Georgia, USA., Chien FL; Department of Pediatrics, Emory University School of Medicine, Atlanta, Georgia, USA., Malhotra A; Department of Pediatrics, Emory University School of Medicine, Atlanta, Georgia, USA., Zhu D; Department of Pediatrics, Emory University School of Medicine, Atlanta, Georgia, USA., Gershon I; Department of Pediatrics, Emory University, Atlanta, Georgia, USA., Zhang H; Department of Pediatrics, Emory University School of Medicine, Atlanta, Georgia, USA., Velazquez Vega JE; Department of Pathology, Children's Healthcare of Atlanta, Atlanta, Georgia, USA., Schniederjan M; Department of Pathology, Children's Healthcare of Atlanta, Atlanta, Georgia, USA., Sposito T; Division of Regenerative Medicine, Department of Medicine, Moores Cancer Center and Sanford Stem Cell Institute, UC San Diego, La Jolla, California, USA., Adams PD; Cancer Genome and Epigenetics Program, NCI-Designated Cancer Center, Sanford Burnham Prebys Medical Discovery Institute, La Jolla, California, USA., Allen JE; Chimerix (a Jazz Pharmaceuticals Company), Durham, North Carolina, USA., Prabhu VV; Chimerix (a Jazz Pharmaceuticals Company), Durham, North Carolina, USA., Wechsler-Reya RJ; Department of Neurology and Herbert Irving Comprehensive Cancer Center, Columbia University Medical Center, New York, New York, USA., MacDonald TJ; Cancer Genome and Epigenetics Program, NCI-Designated Cancer Center, Sanford Burnham Prebys Medical Discovery Institute, La Jolla, California, USA.; Aflac Cancer and Blood Disorders Center, Children's Healthcare of Atlanta, Atlanta, Georgia, USA.
Source: Neuro-oncology [Neuro Oncol] 2026 Jul 01; Vol. 28 (7), pp. 1753-1768.
Publication Type: Journal Article
Journal Info: Publisher: Oxford University Press Country of Publication: England NLM ID: 100887420 Publication Model: Print Cited Medium: Internet ISSN: 1523-5866 (Electronic) Linking ISSN: 15228517 NLM ISO Abbreviation: Neuro Oncol Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1523-5866
DOI:10.1093/neuonc/noag053