Gene-sized editing for the therapy of genetic diseases.

Saved in:
Bibliographic Details
Title: Gene-sized editing for the therapy of genetic diseases.
Authors: Padureanu T; Genomics Research and Development Institute, Bucharest, Romania.; Faculty of Medicine, Carol Davila University of Medicine and Pharmacy, Bucharest, Romania., Cocoș R; Genomics Research and Development Institute, Bucharest, Romania. relu.cocos@umfcd.ro.; Faculty of Medicine, Carol Davila University of Medicine and Pharmacy, Bucharest, Romania. relu.cocos@umfcd.ro., Matache IM; Faculty of Medicine, Carol Davila University of Medicine and Pharmacy, Bucharest, Romania., Bucur O; Genomics Research and Development Institute, Bucharest, Romania. octavian.bucur@genomica.gov.ro.; Faculty of Medicine, Carol Davila University of Medicine and Pharmacy, Bucharest, Romania. octavian.bucur@genomica.gov.ro.; Viron Molecular Medicine Institute, Boston, MA, USA. octavian.bucur@genomica.gov.ro.
Source: Functional & integrative genomics [Funct Integr Genomics] 2026 Mar 13; Vol. 26 (1). Date of Electronic Publication: 2026 Mar 13.
Publication Type: Journal Article; Review
Journal Info: Publisher: Springer Country of Publication: Germany NLM ID: 100939343 Publication Model: Electronic Cited Medium: Internet ISSN: 1438-7948 (Electronic) Linking ISSN: 1438793X NLM ISO Abbreviation: Funct Integr Genomics Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1438-7948
DOI:10.1007/s10142-026-01823-1