Toxicologic Pathology Forum: Opinion on Considerations for Determination of Adverse Versus Nonadverse Nerve Fiber Degeneration in Nonclinical Toxicity Studies of Oligonucleotides Delivered Directly Into the Intrathecal Space.

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Title: Toxicologic Pathology Forum: Opinion on Considerations for Determination of Adverse Versus Nonadverse Nerve Fiber Degeneration in Nonclinical Toxicity Studies of Oligonucleotides Delivered Directly Into the Intrathecal Space.
Authors: Berman-Booty LD; Ionis Pharmaceuticals, Carlsbad, California, USA., Pardo ID; Biogen, Inc., Cambridge, Massachusetts, USA., Bolon B; GEMpath, Inc., Longmont, Colorado, USA., Singh K; Wave Life Sciences, Cambridge, Massachusetts, USA., Morrison JP; Charles River Laboratories, Shrewsbury, Massachusetts, USA., Patrick S; Alnylam Pharmaceuticals, Inc., Cambridge, Massachusetts, USA., Cramer S; StageBio, Frederick, Maryland, USA., Grieves JL; Ionis Pharmaceuticals, Carlsbad, California, USA.
Source: Toxicologic pathology [Toxicol Pathol] 2026 Jun; Vol. 54 (4), pp. 327-338. Date of Electronic Publication: 2026 Mar 25.
Publication Type: Journal Article
Journal Info: Publisher: Sage Publications Country of Publication: United States NLM ID: 7905907 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1533-1601 (Electronic) Linking ISSN: 01926233 NLM ISO Abbreviation: Toxicol Pathol Subsets: MEDLINE
Database: MEDLINE Ultimate
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ISSN:1533-1601
DOI:10.1177/01926233261430687