Emicizumab prophylaxis beyond clinical trials: a multicenter, prospective real-world study of pediatric hemophilia patients with and without inhibitors.

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Bibliographic Details
Title: Emicizumab prophylaxis beyond clinical trials: a multicenter, prospective real-world study of pediatric hemophilia patients with and without inhibitors.
Authors: Sherief LM; Pediatric Hematology and Oncology Unit, Pediatric Department, Faculty of Medicine, Zagazig University, Zagazig, Egypt. lamesh25@yahoo.com., Elagamy O; Department of Pediatrics, Faculty of Medicine, Kafrelsheikh University, Kafrelsheikh, Egypt., Darwish A; Pediatric Hematology and Oncology Unit, Pediatric Department, Faculty of Medicine, Mansoura University, Mansoura, Egypt., Soliman NK; Pediatric Hematology and Oncology Unit, Pediatric Department, Faculty of Medicine, Zagazig University, Zagazig, Egypt., Elgendy MR; Pediatric Department, Mabara Health Insurance Hospital, Zagazig, Egypt., Nazim A; Pediatric Department, Mansoura Health Insurance Hospital, Mansoura, Egypt., Sobhi A; Department of Pediatrics, Faculty of Medicine, Kafrelsheikh University, Kafrelsheikh, Egypt.
Source: European journal of pediatrics [Eur J Pediatr] 2026 Apr 11; Vol. 185 (5). Date of Electronic Publication: 2026 Apr 11.
Publication Type: Journal Article; Multicenter Study
Journal Info: Publisher: Springer Verlag Country of Publication: Germany NLM ID: 7603873 Publication Model: Electronic Cited Medium: Internet ISSN: 1432-1076 (Electronic) Linking ISSN: 03406199 NLM ISO Abbreviation: Eur J Pediatr Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1432-1076
DOI:10.1007/s00431-026-06872-z