Gene Editing for Haemophilia-The Next Frontier.

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Bibliographic Details
Title: Gene Editing for Haemophilia-The Next Frontier.
Authors: Pinotti M; Department of Life Sciences and Biotechnology, University of Ferrara, Ferrara, Emilia-Romagna, Italy., Newby GA; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.; Institute of NanoBioTechnology, Johns Hopkins University, Baltimore, Maryland, USA., Selvaraj S; Department of Pediatrics, University of Michigan, Ann Arbor, Michigan, USA., Pipe SW; Departments of Pediatrics and Pathology, University of Michigan, Ann Arbor, Michigan, USA.
Source: Haemophilia : the official journal of the World Federation of Hemophilia [Haemophilia] 2026 Apr 16. Date of Electronic Publication: 2026 Apr 16.
Publication Type: Journal Article
Journal Info: Publisher: Blackwell Science Country of Publication: England NLM ID: 9442916 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1365-2516 (Electronic) Linking ISSN: 13518216 NLM ISO Abbreviation: Haemophilia Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1365-2516
DOI:10.1111/hae.70238