Gene Editing for Haemophilia-The Next Frontier.

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Title: Gene Editing for Haemophilia-The Next Frontier.
Authors: Pinotti M; Department of Life Sciences and Biotechnology, University of Ferrara, Ferrara, Emilia-Romagna, Italy., Newby GA; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.; Institute of NanoBioTechnology, Johns Hopkins University, Baltimore, Maryland, USA., Selvaraj S; Department of Pediatrics, University of Michigan, Ann Arbor, Michigan, USA., Pipe SW; Departments of Pediatrics and Pathology, University of Michigan, Ann Arbor, Michigan, USA.
Source: Haemophilia : the official journal of the World Federation of Hemophilia [Haemophilia] 2026 Apr 16. Date of Electronic Publication: 2026 Apr 16.
Publication Type: Journal Article
Journal Info: Publisher: Blackwell Science Country of Publication: England NLM ID: 9442916 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1365-2516 (Electronic) Linking ISSN: 13518216 NLM ISO Abbreviation: Haemophilia Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Availability: 0
Header DbId: mdl
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An: 41988847
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PubType: Academic Journal
PubTypeId: academicJournal
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  Data: Gene Editing for Haemophilia-The Next Frontier.
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  Data: <searchLink fieldCode="AU" term="%22Pinotti+M%22">Pinotti M</searchLink>; Department of Life Sciences and Biotechnology, University of Ferrara, Ferrara, Emilia-Romagna, Italy.<br /><searchLink fieldCode="AU" term="%22Newby+GA%22">Newby GA</searchLink>; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.; Institute of NanoBioTechnology, Johns Hopkins University, Baltimore, Maryland, USA.<br /><searchLink fieldCode="AU" term="%22Selvaraj+S%22">Selvaraj S</searchLink>; Department of Pediatrics, University of Michigan, Ann Arbor, Michigan, USA.<br /><searchLink fieldCode="AU" term="%22Pipe+SW%22">Pipe SW</searchLink>; Departments of Pediatrics and Pathology, University of Michigan, Ann Arbor, Michigan, USA.
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  Data: <searchLink fieldCode="JN" term="%229442916%22">Haemophilia : the official journal of the World Federation of Hemophilia</searchLink> [Haemophilia] 2026 Apr 16. <i>Date of Electronic Publication: </i>2026 Apr 16.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Blackwell+Science%22">Blackwell Science </searchLink><i>Country of Publication: </i>England <i>NLM ID: </i>9442916 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1365-2516 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2213518216%22">13518216 </searchLink><i>NLM ISO Abbreviation: </i>Haemophilia <i>Subsets: </i>MEDLINE
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=41988847
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        Value: 10.1111/hae.70238
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      – Code: eng
        Text: English
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      – TitleFull: Gene Editing for Haemophilia-The Next Frontier.
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            NameFull: Pinotti M
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            NameFull: Newby GA
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            NameFull: Selvaraj S
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            NameFull: Pipe SW
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            – D: 16
              M: 04
              Text: 2026 Apr 16
              Type: published
              Y: 2026
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              Value: 1365-2516
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            – TitleFull: Haemophilia : the official journal of the World Federation of Hemophilia
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