The Placebo Effect in Rare Disease Clinical Trials: Measurement, Impact, and Statistical Approaches for Patient-as-Own-Control Designs.
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| Title: | The Placebo Effect in Rare Disease Clinical Trials: Measurement, Impact, and Statistical Approaches for Patient-as-Own-Control Designs. |
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| Authors: | Summar ML; George Washington University, Washington, DC, USA.; Uncommon Cures, Chevy Chase, Maryland, USA., Woodcock J; Center for Drug Evaluation and Research, U.S. Food and Drug Administration, Brookeville, Maryland, USA. |
| Source: | Clinical and translational science [Clin Transl Sci] 2026 May; Vol. 19 (5), pp. e70550. |
| Publication Type: | Journal Article; Review |
| Journal Info: | Publisher: WileyBlackwell Pub Country of Publication: United States NLM ID: 101474067 Publication Model: Print Cited Medium: Internet ISSN: 1752-8062 (Electronic) Linking ISSN: 17528054 NLM ISO Abbreviation: Clin Transl Sci Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| ISSN: | 1752-8062 |
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| DOI: | 10.1111/cts.70550 |