| Authors: |
Heezen LG; Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands., Mao Q; Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands., Nicolau S; Center for Gene Therapy, The Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, OH, USA., Rausell CN; Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands., van der Weerd J; Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands., Kueckelhaus J; Microenvironment and Immunology Research Laboratory, Medical Center, Faculty of Medicine, Freiburg University, Freiburg, Germany.; Department of Neurosurgery, Medical Center, Faculty of Medicine, Erlangen University, Erlangen, Germany., Gokul Nath R; John Walton Muscular Dystrophy Research Centre, Newcastle University Translational and Clinical Research Institute, Newcastle Upon Tyne NHS Trust, Newcastle Upon Tyne, UK., Diaz-Manera J; John Walton Muscular Dystrophy Research Centre, Newcastle University Translational and Clinical Research Institute, Newcastle Upon Tyne NHS Trust, Newcastle Upon Tyne, UK.; Laboratori de Malalties Neuromusculars, Institu de recerca Hospital Sant Pau, Barcelona, Spain.; Centro de Investigación Biomédica en red de enfermedades raras (CIBERER), Madrid, Spain., Kan HE; Department of Radiology, Leiden University Medical Center, Leiden, The Netherlands.; Duchenne Center, The Netherlands., Niks EH; Duchenne Center, The Netherlands.; Department of Neurology, Leiden University Medical Center, Leiden, The Netherlands., van Putten M; Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands.; Duchenne Center, The Netherlands., Aartsma-Rus A; Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands.; Duchenne Center, The Netherlands., Flanigan KM; Center for Gene Therapy, The Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, OH, USA.; Department of Pediatrics, The Ohio State University, Columbus, OH, USA.; Department of Neurology, The Ohio State University, Columbus, OH, USA., Mahfouz A; Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands.; Delft Bioinformatics Lab, Delft University of Technology, Delft, The Netherlands., Spitali P; Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands.; Duchenne Center, The Netherlands. |