Trial-ready external controls for gene therapy: The MATCH cohort in maple syrup urine disease.

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Bibliographic Details
Title: Trial-ready external controls for gene therapy: The MATCH cohort in maple syrup urine disease.
Authors: Brigatti KW; Clinic for Special Children, Gordonville, PA 17529, USA., Rodrigues A; Clinic for Special Children, Gordonville, PA 17529, USA., Sweigert E; Clinic for Special Children, Gordonville, PA 17529, USA., Williamson J; Clinic for Special Children, Gordonville, PA 17529, USA., Koehler A; Clinic for Special Children, Gordonville, PA 17529, USA., Meier GL; Clinic for Special Children, Gordonville, PA 17529, USA., Poskitt LE; Clinic for Special Children, Gordonville, PA 17529, USA., Carson VJ; Clinic for Special Children, Gordonville, PA 17529, USA., Robinson D; Clinic for Special Children, Gordonville, PA 17529, USA., Strauss KA; Clinic for Special Children, Gordonville, PA 17529, USA; Plowshare Therapies, Lancaster, PA 17603, USA. Electronic address: kastrauss@plowsharetherapies.com.
Source: Cell reports. Medicine [Cell Rep Med] 2026 Jun 16; Vol. 7 (6), pp. 102799. Date of Electronic Publication: 2026 May 12.
Publication Type: Journal Article
Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 101766894 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2666-3791 (Electronic) Linking ISSN: 26663791 NLM ISO Abbreviation: Cell Rep Med Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:2666-3791
DOI:10.1016/j.xcrm.2026.102799