MicroRNA-based targeting strategies enable AAV-mediated, tissue-selective gene expression in adipose tissue and skeletal muscle of mice.

Saved in:
Bibliographic Details
Title: MicroRNA-based targeting strategies enable AAV-mediated, tissue-selective gene expression in adipose tissue and skeletal muscle of mice.
Authors: Blahetek G; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, Biberach an der Riß, Germany., Abele S; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, Biberach an der Riß, Germany., Schmierer E; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, Biberach an der Riß, Germany., Matera D; Global Cardio-Renal-Metabolic Diseases Research, Boehringer Ingelheim Pharmaceuticals, Inc., Ridgefield, CT, USA., Geisbauer A; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, Biberach an der Riß, Germany., Lempp C; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, Biberach an der Riß, Germany., Schönberger T; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, Biberach an der Riß, Germany., Holdenried-Krafft S; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, Biberach an der Riß, Germany., Gross P; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, Biberach an der Riß, Germany., Strobel B; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, Biberach an der Riß, Germany.
Source: Molecular therapy. Advances [Mol Ther Adv] 2025 Dec 26; Vol. 34 (1), pp. 201664. Date of Electronic Publication: 2025 Dec 26 (Print Publication: 2026).
Publication Type: Journal Article
Journal Info: Country of Publication: United States NLM ID: 9919257804006676 Publication Model: eCollection Cited Medium: Internet ISSN: 3117-387X (Electronic) Linking ISSN: 3117387X NLM ISO Abbreviation: Mol Ther Adv Subsets: PubMed not MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:3117-387X
DOI:10.1016/j.omta.2025.201664