Validation of a torsinA cerebellar knockdown model of DYT1 dystonia.

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Title: Validation of a torsinA cerebellar knockdown model of DYT1 dystonia.
Authors: Liu Y; Norman Fixel Institute for Neurological Diseases, McKnight Brain Institute, Department of Neurology, College of Medicine, University of Florida, Gainesville, FL, 32610, USA.; College of Biological Science and Technology, Beijing Forestry University, Beijing 100083, PR China., Xing H; Norman Fixel Institute for Neurological Diseases, McKnight Brain Institute, Department of Neurology, College of Medicine, University of Florida, Gainesville, FL, 32610, USA., Yokoi F; Norman Fixel Institute for Neurological Diseases, McKnight Brain Institute, Department of Neurology, College of Medicine, University of Florida, Gainesville, FL, 32610, USA., Walker AL; Norman Fixel Institute for Neurological Diseases, McKnight Brain Institute, Department of Neurology, College of Medicine, University of Florida, Gainesville, FL, 32610, USA., Chen D; Norman Fixel Institute for Neurological Diseases, McKnight Brain Institute, Department of Neurology, College of Medicine, University of Florida, Gainesville, FL, 32610, USA., Rodriguez-Lebron E; Department of Pharmacology and Therapeutics, College of Medicine, University of Florida, Gainesville, FL, 32610, USA., Li Y; Norman Fixel Institute for Neurological Diseases, McKnight Brain Institute, Department of Neurology, College of Medicine, University of Florida, Gainesville, FL, 32610, USA.
Source: Dystonia (Lausanne, Switzerland) [Dystonia] 2026; Vol. 5. Date of Electronic Publication: 2026 Feb 09.
Publication Type: Journal Article
Journal Info: Publisher: Frontiers Media S.A Country of Publication: Switzerland NLM ID: 9918486684106676 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2813-2106 (Electronic) Linking ISSN: 28132106 NLM ISO Abbreviation: Dystonia Subsets: PubMed not MEDLINE
Database: MEDLINE Ultimate
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ISSN:2813-2106
DOI:10.3389/dyst.2026.14631