A Randomized, Double-Blind, Pilot Study of N-Acetylcysteine for Motor and Cognitive Symptoms in Youth With Neurofibromatosis Type 1.

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Bibliographic Details
Title: A Randomized, Double-Blind, Pilot Study of N-Acetylcysteine for Motor and Cognitive Symptoms in Youth With Neurofibromatosis Type 1.
Authors: Gilbert DL; Division of Neurology, Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio; Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, Ohio. Electronic address: Donald.gilbert@cchmc.org., Aschbacher-Smith LE; Division of Genetics, Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio., Migneault KY; Division of Neurology, Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio., Huddleston DA; Division of Neurology, Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio., Cecil KM; Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, Ohio; Department of Radiology, Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio., Beebe DW; Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, Ohio; Division of Behavioral Medicine and Clinical Psychology, Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio., Zhang B; Department of Radiology, Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio., Ratner N; Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, Ohio; Division of Experimental Hematology and Cancer Biology, Cincinnati Children's Hospital, Cincinnati, Ohio., Prada CE; Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, Ohio; Division of Genetics, Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio.
Source: Pediatric neurology [Pediatr Neurol] 2026 Jul; Vol. 180, pp. 129-137. Date of Electronic Publication: 2026 May 05.
Publication Type: Journal Article; Randomized Controlled Trial
Journal Info: Publisher: Elsevier Science Publishing Country of Publication: United States NLM ID: 8508183 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1873-5150 (Electronic) Linking ISSN: 08878994 NLM ISO Abbreviation: Pediatr Neurol Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1873-5150
DOI:10.1016/j.pediatrneurol.2026.04.024