Updated EBMT/ESID inborn errors working party guidelines for haematopoietic stem cell transplantation for inborn errors of immunity and metabolism.

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Title: Updated EBMT/ESID inborn errors working party guidelines for haematopoietic stem cell transplantation for inborn errors of immunity and metabolism.
Authors: Albert MH; Department of Pediatrics, Dr. von Hauner Children's Hospital, University Hospital, LMU, Munich, Germany. malbert@med.lmu.de., Lankester AC; Department of Pediatrics, Willem-Alexander Children's Hospital, Leiden University Medical Center, Leiden, The Netherlands., Wynn R; Blood and Marrow Transplant Programme, Royal Manchester Children's Hospital, Manchester, UK., Gennery AR; Translational and Clinical Research Institute, Newcastle University, and Paediatric Immunology and Haematopoietic Stem Cell Transplantation, Great North Children's Hospital, Newcastle upon Tyne, UK., Hoenig M; Department of Pediatrics, University Medical Center Ulm, Ulm, Germany., Kreins A; Infection Immunity and Inflammation Research and Teaching Department, University College London Great Ormond Street Institute of Child Health, London, UK.; Department of Immunology and Gene Therapy, Great Ormond Street Hospital for Children NHS Foundation Trust, London, UK., Morris EC; UCL Institute of Immunity and Transplantation, UCL, London, UK.; Department of Haematology, University College London Hospitals NHS Foundation Trust, London, UK.; Department of Immunology, Royal Free London Hospitals NHS Foundation Trust, London, UK., Slatter M; Translational and Clinical Research Institute, Newcastle University, and Paediatric Immunology and Haematopoietic Stem Cell Transplantation, Great North Children's Hospital, Newcastle upon Tyne, UK., Bernardo ME; Pediatric Immunohematology and Bone Marrow Transplantation, IRCCS San Raffaele Scientific Institute, Milan; San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), Milan, 'Vita-Salute' San Raffaele University, Milan, Italy., Neven B; Pediatric Unit of Immunology, Hematology, and Rheumatology, Necker Hospital, Paris, France.; IMAGINE Institute U1163, Paris, France; Paris Cité University, Paris, France.
Corporate Authors: Inborn Errors Working Party of the European Society for Blood and Marrow Transplantation and the European Society for Immune Deficiencies, and the European Reference Network on Rare Primary Immunodeficiency Autoinflammatory Autoimmune diseases (RITA)
Source: Bone marrow transplantation [Bone Marrow Transplant] 2026 Jul; Vol. 61 (7), pp. 791-804. Date of Electronic Publication: 2026 May 22.
Publication Type: Journal Article; Review
Journal Info: Publisher: Nature Publishing Group Country of Publication: England NLM ID: 8702459 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1476-5365 (Electronic) Linking ISSN: 02683369 NLM ISO Abbreviation: Bone Marrow Transplant Subsets: MEDLINE; In Process
Database: MEDLINE Ultimate
Description
ISSN:1476-5365
DOI:10.1038/s41409-026-02906-0