Vutrisiran-Mediated Knockdown of Transthyretin in Patients with ATTR Amyloidosis.

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Bibliographic Details
Title: Vutrisiran-Mediated Knockdown of Transthyretin in Patients with ATTR Amyloidosis.
Authors: Fontana M; National Amyloidosis Centre, UCL, Division of Medicine, University College London, Royal Free Hospital, Pond Street, London, NW3 2QG, UK. marianna.fontana@nhs.net., Algalarrondo V; French Reference Centre for Cardiac Amyloidosis Ceramic-Cardio, Department of Cardiology, Bichat University Hospital, AP-HP, Paris, France., Garcia-Pavia P; Department of Cardiology, Hospital Universitario Puerta de Hierro Majadahonda, IDIPHISA, CIBERCV, and Centro Nacional de Investigaciones Cardiovasculares (CNIC), Madrid, Spain., Maurer MS; Department of Medicine, Columbia University Irving Medical Center, New York, NY, USA., Gillmore JD; National Amyloidosis Centre, UCL, Division of Medicine, University College London, Royal Free Hospital, Pond Street, London, NW3 2QG, UK., Cappelli F; Tuscan Regional Amyloidosis Centre and Cardiomyopathy Unit, Careggi University Hospital, University of Florence, Florence, Italy., Kolachana K; Alnylam Pharmaceuticals, Cambridge, MA, USA., Gao X; Alnylam Pharmaceuticals, Cambridge, MA, USA., Jadhav S; Alnylam Pharmaceuticals, Cambridge, MA, USA., Mehrotra N; Alnylam Pharmaceuticals, Cambridge, MA, USA., Robbie G; Alnylam Pharmaceuticals, Cambridge, MA, USA., Badri P; Alnylam Pharmaceuticals, Cambridge, MA, USA.
Source: Clinical pharmacokinetics [Clin Pharmacokinet] 2026 Jul; Vol. 65 (7), pp. 1073-1085. Date of Electronic Publication: 2026 May 27.
Publication Type: Journal Article; Randomized Controlled Trial
Journal Info: Publisher: Country of Publication: Switzerland NLM ID: 7606849 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1179-1926 (Electronic) Linking ISSN: 03125963 NLM ISO Abbreviation: Clin Pharmacokinet Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1179-1926
DOI:10.1007/s40262-026-01651-3