Long-term stability of posttranscriptional genetic silencing of BCL11A using a shmiR vector in Sickle Cell Disease.

Saved in:
Bibliographic Details
Title: Long-term stability of posttranscriptional genetic silencing of BCL11A using a shmiR vector in Sickle Cell Disease.
Authors: Esrick EB; Boston Children's Hospital, Boston, Massachusetts, United States., Lehmann L; Division of Pediatric Hematology/Oncology, Dana-Farber Cancer Institute, Boston, MA, United States., Federico A; Boston Children's Hospital, Boston, MA, Boston, Massachusetts, United States., Vincon H; Boston Children's Hospital, Boston, Massachusetts, United States., Liu B; Boston Children's Hospital, Boston, Massachusetts, United States., Daley H; Dana-Farber Cancer Institute, Boston, Massachusetts, United States., Dansereau C; Dana-Farber Cancer Institute, Boston, Massachusetts, United States., De Oliveira S; University of California, Los Angeles, Los Angeles, California, United States., Everett JK; University of Pennsylvania, Philadelphia, Pennsylvania, United States., Kao PC; Boston Children's Hospital/Dana-Farber Cancer Institute, Boston, Massachusetts, United States., Moore TB; UCLA, Los Angeles, CA, California, United States., Morris E; Dana-Farber Cancer Institute, Boston, Massachusetts, United States., Trebeden-Negre H; CellforCure, Les Ulis, France., Shaw KL; Boston Children's Hospital, Boston, Massachusetts, United States., Roach GD; Seattle Children's Hospital, Seattle, Washington, United States., Ritz J; Dana-Farber Cancer Institute; Harvard Medical School, Boston, Massachusetts, United States., Roche AM; University of Pennsylvania, Philadelphia, Pennsylvania, United States., Silva O; Boston Children's Hospital, Boston, Massachusetts, United States., Grant PE; Boston Children's Hospital, Boston, Massachusetts, United States., Bushman FD; University of Pennsylvania, Philadelphia, Pennsylvania, United States., Kohn DB; University of California, Los Angeles, Los Angeles, California, United States., Jain A; Loma Linda University, Redlands, California, United States., London WB; Boston Children's Hospital, Boston, Massachusetts, United States., Justus DG; Boston Children's Hospital, Canton, Massachusetts, United States., Armant M; boston children's hospital, boston, Massachusetts, United States., Manis JP; Boston Children's Hospital, Boston, Massachusetts, United States., Williams DA; Boston Children's Hospital, Boston, Massachusetts, United States.
Source: Blood [Blood] 2026 Jun 02. Date of Electronic Publication: 2026 Jun 02.
Publication Type: Journal Article
Journal Info: Publisher: Elsevier Country of Publication: United States NLM ID: 7603509 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1528-0020 (Electronic) Linking ISSN: 00064971 NLM ISO Abbreviation: Blood Subsets: MEDLINE
Database: MEDLINE Ultimate
FullText Text:
  Availability: 0
Header DbId: mdl
DbLabel: MEDLINE Ultimate
An: 42233421
AccessLevel: 2
PubType: Academic Journal
PubTypeId: academicJournal
PreciseRelevancyScore: 0
IllustrationInfo
Items – Name: Title
  Label: Title
  Group: Ti
  Data: Long-term stability of posttranscriptional genetic silencing of BCL11A using a shmiR vector in Sickle Cell Disease.
– Name: Author
  Label: Authors
  Group: Au
  Data: <searchLink fieldCode="AU" term="%22Esrick+EB%22">Esrick EB</searchLink>; Boston Children's Hospital, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Lehmann+L%22">Lehmann L</searchLink>; Division of Pediatric Hematology/Oncology, Dana-Farber Cancer Institute, Boston, MA, United States.<br /><searchLink fieldCode="AU" term="%22Federico+A%22">Federico A</searchLink>; Boston Children's Hospital, Boston, MA, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Vincon+H%22">Vincon H</searchLink>; Boston Children's Hospital, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Liu+B%22">Liu B</searchLink>; Boston Children's Hospital, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Daley+H%22">Daley H</searchLink>; Dana-Farber Cancer Institute, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Dansereau+C%22">Dansereau C</searchLink>; Dana-Farber Cancer Institute, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22De+Oliveira+S%22">De Oliveira S</searchLink>; University of California, Los Angeles, Los Angeles, California, United States.<br /><searchLink fieldCode="AU" term="%22Everett+JK%22">Everett JK</searchLink>; University of Pennsylvania, Philadelphia, Pennsylvania, United States.<br /><searchLink fieldCode="AU" term="%22Kao+PC%22">Kao PC</searchLink>; Boston Children's Hospital/Dana-Farber Cancer Institute, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Moore+TB%22">Moore TB</searchLink>; UCLA, Los Angeles, CA, California, United States.<br /><searchLink fieldCode="AU" term="%22Morris+E%22">Morris E</searchLink>; Dana-Farber Cancer Institute, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Trebeden-Negre+H%22">Trebeden-Negre H</searchLink>; CellforCure, Les Ulis, France.<br /><searchLink fieldCode="AU" term="%22Shaw+KL%22">Shaw KL</searchLink>; Boston Children's Hospital, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Roach+GD%22">Roach GD</searchLink>; Seattle Children's Hospital, Seattle, Washington, United States.<br /><searchLink fieldCode="AU" term="%22Ritz+J%22">Ritz J</searchLink>; Dana-Farber Cancer Institute; Harvard Medical School, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Roche+AM%22">Roche AM</searchLink>; University of Pennsylvania, Philadelphia, Pennsylvania, United States.<br /><searchLink fieldCode="AU" term="%22Silva+O%22">Silva O</searchLink>; Boston Children's Hospital, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Grant+PE%22">Grant PE</searchLink>; Boston Children's Hospital, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Bushman+FD%22">Bushman FD</searchLink>; University of Pennsylvania, Philadelphia, Pennsylvania, United States.<br /><searchLink fieldCode="AU" term="%22Kohn+DB%22">Kohn DB</searchLink>; University of California, Los Angeles, Los Angeles, California, United States.<br /><searchLink fieldCode="AU" term="%22Jain+A%22">Jain A</searchLink>; Loma Linda University, Redlands, California, United States.<br /><searchLink fieldCode="AU" term="%22London+WB%22">London WB</searchLink>; Boston Children's Hospital, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Justus+DG%22">Justus DG</searchLink>; Boston Children's Hospital, Canton, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Armant+M%22">Armant M</searchLink>; boston children's hospital, boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Manis+JP%22">Manis JP</searchLink>; Boston Children's Hospital, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Williams+DA%22">Williams DA</searchLink>; Boston Children's Hospital, Boston, Massachusetts, United States.
– Name: TitleSource
  Label: Source
  Group: Src
  Data: <searchLink fieldCode="JN" term="%227603509%22">Blood</searchLink> [Blood] 2026 Jun 02. <i>Date of Electronic Publication: </i>2026 Jun 02.
– Name: TypePub
  Label: Publication Type
  Group: TypPub
  Data: Journal Article
– Name: TitleSource
  Label: Journal Info
  Group: Src
  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Elsevier%22">Elsevier </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>7603509 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1528-0020 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2200064971%22">00064971 </searchLink><i>NLM ISO Abbreviation: </i>Blood <i>Subsets: </i>MEDLINE
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=42233421
RecordInfo BibRecord:
  BibEntity:
    Identifiers:
      – Type: doi
        Value: 10.1182/blood.2026033871
    Languages:
      – Code: eng
        Text: English
    Titles:
      – TitleFull: Long-term stability of posttranscriptional genetic silencing of BCL11A using a shmiR vector in Sickle Cell Disease.
        Type: main
  BibRelationships:
    HasContributorRelationships:
      – PersonEntity:
          Name:
            NameFull: Esrick EB
      – PersonEntity:
          Name:
            NameFull: Lehmann L
      – PersonEntity:
          Name:
            NameFull: Federico A
      – PersonEntity:
          Name:
            NameFull: Vincon H
      – PersonEntity:
          Name:
            NameFull: Liu B
      – PersonEntity:
          Name:
            NameFull: Daley H
      – PersonEntity:
          Name:
            NameFull: Dansereau C
      – PersonEntity:
          Name:
            NameFull: De Oliveira S
      – PersonEntity:
          Name:
            NameFull: Everett JK
      – PersonEntity:
          Name:
            NameFull: Kao PC
      – PersonEntity:
          Name:
            NameFull: Moore TB
      – PersonEntity:
          Name:
            NameFull: Morris E
      – PersonEntity:
          Name:
            NameFull: Trebeden-Negre H
      – PersonEntity:
          Name:
            NameFull: Shaw KL
      – PersonEntity:
          Name:
            NameFull: Roach GD
      – PersonEntity:
          Name:
            NameFull: Ritz J
      – PersonEntity:
          Name:
            NameFull: Roche AM
      – PersonEntity:
          Name:
            NameFull: Silva O
      – PersonEntity:
          Name:
            NameFull: Grant PE
      – PersonEntity:
          Name:
            NameFull: Bushman FD
      – PersonEntity:
          Name:
            NameFull: Kohn DB
      – PersonEntity:
          Name:
            NameFull: Jain A
      – PersonEntity:
          Name:
            NameFull: London WB
      – PersonEntity:
          Name:
            NameFull: Justus DG
      – PersonEntity:
          Name:
            NameFull: Armant M
      – PersonEntity:
          Name:
            NameFull: Manis JP
      – PersonEntity:
          Name:
            NameFull: Williams DA
    IsPartOfRelationships:
      – BibEntity:
          Dates:
            – D: 02
              M: 06
              Text: 2026 Jun 02
              Type: published
              Y: 2026
          Identifiers:
            – Type: issn-electronic
              Value: 1528-0020
          Titles:
            – TitleFull: Blood
              Type: main
ResultId 1