Long-term stability of posttranscriptional genetic silencing of BCL11A using a shmiR vector in Sickle Cell Disease.
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| Title: | Long-term stability of posttranscriptional genetic silencing of BCL11A using a shmiR vector in Sickle Cell Disease. |
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| Authors: | Esrick EB; Boston Children's Hospital, Boston, Massachusetts, United States., Lehmann L; Division of Pediatric Hematology/Oncology, Dana-Farber Cancer Institute, Boston, MA, United States., Federico A; Boston Children's Hospital, Boston, MA, Boston, Massachusetts, United States., Vincon H; Boston Children's Hospital, Boston, Massachusetts, United States., Liu B; Boston Children's Hospital, Boston, Massachusetts, United States., Daley H; Dana-Farber Cancer Institute, Boston, Massachusetts, United States., Dansereau C; Dana-Farber Cancer Institute, Boston, Massachusetts, United States., De Oliveira S; University of California, Los Angeles, Los Angeles, California, United States., Everett JK; University of Pennsylvania, Philadelphia, Pennsylvania, United States., Kao PC; Boston Children's Hospital/Dana-Farber Cancer Institute, Boston, Massachusetts, United States., Moore TB; UCLA, Los Angeles, CA, California, United States., Morris E; Dana-Farber Cancer Institute, Boston, Massachusetts, United States., Trebeden-Negre H; CellforCure, Les Ulis, France., Shaw KL; Boston Children's Hospital, Boston, Massachusetts, United States., Roach GD; Seattle Children's Hospital, Seattle, Washington, United States., Ritz J; Dana-Farber Cancer Institute; Harvard Medical School, Boston, Massachusetts, United States., Roche AM; University of Pennsylvania, Philadelphia, Pennsylvania, United States., Silva O; Boston Children's Hospital, Boston, Massachusetts, United States., Grant PE; Boston Children's Hospital, Boston, Massachusetts, United States., Bushman FD; University of Pennsylvania, Philadelphia, Pennsylvania, United States., Kohn DB; University of California, Los Angeles, Los Angeles, California, United States., Jain A; Loma Linda University, Redlands, California, United States., London WB; Boston Children's Hospital, Boston, Massachusetts, United States., Justus DG; Boston Children's Hospital, Canton, Massachusetts, United States., Armant M; boston children's hospital, boston, Massachusetts, United States., Manis JP; Boston Children's Hospital, Boston, Massachusetts, United States., Williams DA; Boston Children's Hospital, Boston, Massachusetts, United States. |
| Source: | Blood [Blood] 2026 Jun 02. Date of Electronic Publication: 2026 Jun 02. |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Elsevier Country of Publication: United States NLM ID: 7603509 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1528-0020 (Electronic) Linking ISSN: 00064971 NLM ISO Abbreviation: Blood Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 42233421 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Long-term stability of posttranscriptional genetic silencing of BCL11A using a shmiR vector in Sickle Cell Disease. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Esrick+EB%22">Esrick EB</searchLink>; Boston Children's Hospital, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Lehmann+L%22">Lehmann L</searchLink>; Division of Pediatric Hematology/Oncology, Dana-Farber Cancer Institute, Boston, MA, United States.<br /><searchLink fieldCode="AU" term="%22Federico+A%22">Federico A</searchLink>; Boston Children's Hospital, Boston, MA, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Vincon+H%22">Vincon H</searchLink>; Boston Children's Hospital, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Liu+B%22">Liu B</searchLink>; Boston Children's Hospital, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Daley+H%22">Daley H</searchLink>; Dana-Farber Cancer Institute, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Dansereau+C%22">Dansereau C</searchLink>; Dana-Farber Cancer Institute, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22De+Oliveira+S%22">De Oliveira S</searchLink>; University of California, Los Angeles, Los Angeles, California, United States.<br /><searchLink fieldCode="AU" term="%22Everett+JK%22">Everett JK</searchLink>; University of Pennsylvania, Philadelphia, Pennsylvania, United States.<br /><searchLink fieldCode="AU" term="%22Kao+PC%22">Kao PC</searchLink>; Boston Children's Hospital/Dana-Farber Cancer Institute, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Moore+TB%22">Moore TB</searchLink>; UCLA, Los Angeles, CA, California, United States.<br /><searchLink fieldCode="AU" term="%22Morris+E%22">Morris E</searchLink>; Dana-Farber Cancer Institute, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Trebeden-Negre+H%22">Trebeden-Negre H</searchLink>; CellforCure, Les Ulis, France.<br /><searchLink fieldCode="AU" term="%22Shaw+KL%22">Shaw KL</searchLink>; Boston Children's Hospital, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Roach+GD%22">Roach GD</searchLink>; Seattle Children's Hospital, Seattle, Washington, United States.<br /><searchLink fieldCode="AU" term="%22Ritz+J%22">Ritz J</searchLink>; Dana-Farber Cancer Institute; Harvard Medical School, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Roche+AM%22">Roche AM</searchLink>; University of Pennsylvania, Philadelphia, Pennsylvania, United States.<br /><searchLink fieldCode="AU" term="%22Silva+O%22">Silva O</searchLink>; Boston Children's Hospital, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Grant+PE%22">Grant PE</searchLink>; Boston Children's Hospital, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Bushman+FD%22">Bushman FD</searchLink>; University of Pennsylvania, Philadelphia, Pennsylvania, United States.<br /><searchLink fieldCode="AU" term="%22Kohn+DB%22">Kohn DB</searchLink>; University of California, Los Angeles, Los Angeles, California, United States.<br /><searchLink fieldCode="AU" term="%22Jain+A%22">Jain A</searchLink>; Loma Linda University, Redlands, California, United States.<br /><searchLink fieldCode="AU" term="%22London+WB%22">London WB</searchLink>; Boston Children's Hospital, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Justus+DG%22">Justus DG</searchLink>; Boston Children's Hospital, Canton, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Armant+M%22">Armant M</searchLink>; boston children's hospital, boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Manis+JP%22">Manis JP</searchLink>; Boston Children's Hospital, Boston, Massachusetts, United States.<br /><searchLink fieldCode="AU" term="%22Williams+DA%22">Williams DA</searchLink>; Boston Children's Hospital, Boston, Massachusetts, United States. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%227603509%22">Blood</searchLink> [Blood] 2026 Jun 02. <i>Date of Electronic Publication: </i>2026 Jun 02. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Elsevier%22">Elsevier </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>7603509 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1528-0020 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2200064971%22">00064971 </searchLink><i>NLM ISO Abbreviation: </i>Blood <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=42233421 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1182/blood.2026033871 Languages: – Code: eng Text: English Titles: – TitleFull: Long-term stability of posttranscriptional genetic silencing of BCL11A using a shmiR vector in Sickle Cell Disease. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Esrick EB – PersonEntity: Name: NameFull: Lehmann L – PersonEntity: Name: NameFull: Federico A – PersonEntity: Name: NameFull: Vincon H – PersonEntity: Name: NameFull: Liu B – PersonEntity: Name: NameFull: Daley H – PersonEntity: Name: NameFull: Dansereau C – PersonEntity: Name: NameFull: De Oliveira S – PersonEntity: Name: NameFull: Everett JK – PersonEntity: Name: NameFull: Kao PC – PersonEntity: Name: NameFull: Moore TB – PersonEntity: Name: NameFull: Morris E – PersonEntity: Name: NameFull: Trebeden-Negre H – PersonEntity: Name: NameFull: Shaw KL – PersonEntity: Name: NameFull: Roach GD – PersonEntity: Name: NameFull: Ritz J – PersonEntity: Name: NameFull: Roche AM – PersonEntity: Name: NameFull: Silva O – PersonEntity: Name: NameFull: Grant PE – PersonEntity: Name: NameFull: Bushman FD – PersonEntity: Name: NameFull: Kohn DB – PersonEntity: Name: NameFull: Jain A – PersonEntity: Name: NameFull: London WB – PersonEntity: Name: NameFull: Justus DG – PersonEntity: Name: NameFull: Armant M – PersonEntity: Name: NameFull: Manis JP – PersonEntity: Name: NameFull: Williams DA IsPartOfRelationships: – BibEntity: Dates: – D: 02 M: 06 Text: 2026 Jun 02 Type: published Y: 2026 Identifiers: – Type: issn-electronic Value: 1528-0020 Titles: – TitleFull: Blood Type: main |
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