Meeting report: 2025 muscular dystrophy association summit on 'safety and challenges in gene therapy of neuromuscular diseases'.

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Title: Meeting report: 2025 muscular dystrophy association summit on 'safety and challenges in gene therapy of neuromuscular diseases'.
Authors: Lin BC; Muscular Dystrophy Association, Chicago, IL, USA., Lek A; Muscular Dystrophy Association, Chicago, IL, USA., Bönnemann CG; Department of Genomic and Translational Neuroscience, St. Jude Children's Research Hospital, Memphis, TN, USA., Byrne BJ; Department of Pediatrics and Powell Gene Therapy Center, University of Florida, Gainesville, FL, USA.
Source: Journal of neuromuscular diseases [J Neuromuscul Dis] 2026 Jun 13, pp. 22143602261453651. Date of Electronic Publication: 2026 Jun 13.
Publication Type: Journal Article
Journal Info: Publisher: IOS Press Country of Publication: United States NLM ID: 101649948 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2214-3602 (Electronic) Linking ISSN: 22143599 NLM ISO Abbreviation: J Neuromuscul Dis Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Meeting report: 2025 muscular dystrophy association summit on 'safety and challenges in gene therapy of neuromuscular diseases'.
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  Data: <searchLink fieldCode="AU" term="%22Lin+BC%22">Lin BC</searchLink>; Muscular Dystrophy Association, Chicago, IL, USA.<br /><searchLink fieldCode="AU" term="%22Lek+A%22">Lek A</searchLink>; Muscular Dystrophy Association, Chicago, IL, USA.<br /><searchLink fieldCode="AU" term="%22Bönnemann+CG%22">Bönnemann CG</searchLink>; Department of Genomic and Translational Neuroscience, St. Jude Children's Research Hospital, Memphis, TN, USA.<br /><searchLink fieldCode="AU" term="%22Byrne+BJ%22">Byrne BJ</searchLink>; Department of Pediatrics and Powell Gene Therapy Center, University of Florida, Gainesville, FL, USA.
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  Data: <searchLink fieldCode="JN" term="%22101649948%22">Journal of neuromuscular diseases</searchLink> [J Neuromuscul Dis] 2026 Jun 13, pp. 22143602261453651. <i>Date of Electronic Publication: </i>2026 Jun 13.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22IOS+Press%22">IOS Press </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101649948 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>2214-3602 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2222143599%22">22143599 </searchLink><i>NLM ISO Abbreviation: </i>J Neuromuscul Dis <i>Subsets: </i>MEDLINE
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        Value: 10.1177/22143602261453651
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        Text: English
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        StartPage: 22143602261453651
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      – TitleFull: Meeting report: 2025 muscular dystrophy association summit on 'safety and challenges in gene therapy of neuromuscular diseases'.
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            NameFull: Lin BC
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            NameFull: Lek A
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            NameFull: Bönnemann CG
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          Dates:
            – D: 13
              M: 06
              Text: 2026 Jun 13
              Type: published
              Y: 2026
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