Meeting report: 2025 muscular dystrophy association summit on 'safety and challenges in gene therapy of neuromuscular diseases'.
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| Title: | Meeting report: 2025 muscular dystrophy association summit on 'safety and challenges in gene therapy of neuromuscular diseases'. |
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| Authors: | Lin BC; Muscular Dystrophy Association, Chicago, IL, USA., Lek A; Muscular Dystrophy Association, Chicago, IL, USA., Bönnemann CG; Department of Genomic and Translational Neuroscience, St. Jude Children's Research Hospital, Memphis, TN, USA., Byrne BJ; Department of Pediatrics and Powell Gene Therapy Center, University of Florida, Gainesville, FL, USA. |
| Source: | Journal of neuromuscular diseases [J Neuromuscul Dis] 2026 Jun 13, pp. 22143602261453651. Date of Electronic Publication: 2026 Jun 13. |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: IOS Press Country of Publication: United States NLM ID: 101649948 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2214-3602 (Electronic) Linking ISSN: 22143599 NLM ISO Abbreviation: J Neuromuscul Dis Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
| FullText | Links: – Type: pdflink Text: Availability: 0 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 42287226 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Meeting report: 2025 muscular dystrophy association summit on 'safety and challenges in gene therapy of neuromuscular diseases'. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Lin+BC%22">Lin BC</searchLink>; Muscular Dystrophy Association, Chicago, IL, USA.<br /><searchLink fieldCode="AU" term="%22Lek+A%22">Lek A</searchLink>; Muscular Dystrophy Association, Chicago, IL, USA.<br /><searchLink fieldCode="AU" term="%22Bönnemann+CG%22">Bönnemann CG</searchLink>; Department of Genomic and Translational Neuroscience, St. Jude Children's Research Hospital, Memphis, TN, USA.<br /><searchLink fieldCode="AU" term="%22Byrne+BJ%22">Byrne BJ</searchLink>; Department of Pediatrics and Powell Gene Therapy Center, University of Florida, Gainesville, FL, USA. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22101649948%22">Journal of neuromuscular diseases</searchLink> [J Neuromuscul Dis] 2026 Jun 13, pp. 22143602261453651. <i>Date of Electronic Publication: </i>2026 Jun 13. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22IOS+Press%22">IOS Press </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101649948 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>2214-3602 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2222143599%22">22143599 </searchLink><i>NLM ISO Abbreviation: </i>J Neuromuscul Dis <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=42287226 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1177/22143602261453651 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: 22143602261453651 Titles: – TitleFull: Meeting report: 2025 muscular dystrophy association summit on 'safety and challenges in gene therapy of neuromuscular diseases'. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Lin BC – PersonEntity: Name: NameFull: Lek A – PersonEntity: Name: NameFull: Bönnemann CG – PersonEntity: Name: NameFull: Byrne BJ IsPartOfRelationships: – BibEntity: Dates: – D: 13 M: 06 Text: 2026 Jun 13 Type: published Y: 2026 Identifiers: – Type: issn-electronic Value: 2214-3602 Titles: – TitleFull: Journal of neuromuscular diseases Type: main |
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