Meeting report: 2025 muscular dystrophy association summit on 'safety and challenges in gene therapy of neuromuscular diseases'.

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Bibliographic Details
Title: Meeting report: 2025 muscular dystrophy association summit on 'safety and challenges in gene therapy of neuromuscular diseases'.
Authors: Lin BC; Muscular Dystrophy Association, Chicago, IL, USA., Lek A; Muscular Dystrophy Association, Chicago, IL, USA., Bönnemann CG; Department of Genomic and Translational Neuroscience, St. Jude Children's Research Hospital, Memphis, TN, USA., Byrne BJ; Department of Pediatrics and Powell Gene Therapy Center, University of Florida, Gainesville, FL, USA.
Source: Journal of neuromuscular diseases [J Neuromuscul Dis] 2026 Jun 13, pp. 22143602261453651. Date of Electronic Publication: 2026 Jun 13.
Publication Type: Journal Article
Journal Info: Publisher: IOS Press Country of Publication: United States NLM ID: 101649948 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2214-3602 (Electronic) Linking ISSN: 22143599 NLM ISO Abbreviation: J Neuromuscul Dis Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:2214-3602
DOI:10.1177/22143602261453651