Advances in Gene and Cellular Therapy in Friedreich Ataxia.

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Bibliographic Details
Title: Advances in Gene and Cellular Therapy in Friedreich Ataxia.
Authors: Lazaropoulos MP; Lewis Katz School of Medicine, Temple University, Philadelphia, PA, USA., Lynch DR; The Children's Hospital of Philadelphia (CHOP), 502 Abramson, Philadelphia, PA, 19104, USA. lynchd@pennmedicince.upenn.edu.; University of Pennsylvania School of Medicine, Philadelphia, PA, USA. lynchd@pennmedicince.upenn.edu.
Source: Molecular diagnosis & therapy [Mol Diagn Ther] 2026 Jun 29. Date of Electronic Publication: 2026 Jun 29.
Publication Type: Journal Article; Review
Journal Info: Publisher: Adis, Springer International Country of Publication: New Zealand NLM ID: 101264260 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1179-2000 (Electronic) Linking ISSN: 11771062 NLM ISO Abbreviation: Mol Diagn Ther Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1179-2000
DOI:10.1007/s40291-026-00854-5