Effectiveness and probability of full disease control with canakinumab in familial Mediterranean fever: real-world data from the AIDA Network.

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Title: Effectiveness and probability of full disease control with canakinumab in familial Mediterranean fever: real-world data from the AIDA Network.
Authors: Vitale A; Department of Medical Sciences, Surgery and Neurosciences, Research Center of Systemic Autoinflammatory Diseases and Behçet's Disease Clinic, University of Siena, Siena, Italy.; Azienda Ospedaliero-Universitaria Senese [European Reference Network (ERN) for Rare Immunodeficiency, Autoinflammatory and Autoimmune Diseases (RITA) Center] Siena, Italy., Caggiano V; Department of Medical Sciences, Surgery and Neurosciences, Research Center of Systemic Autoinflammatory Diseases and Behçet's Disease Clinic, University of Siena, Siena, Italy.; Azienda Ospedaliero-Universitaria Senese [European Reference Network (ERN) for Rare Immunodeficiency, Autoinflammatory and Autoimmune Diseases (RITA) Center] Siena, Italy., Sbalchiero J; Department of Medical Sciences, Surgery and Neurosciences, Research Center of Systemic Autoinflammatory Diseases and Behçet's Disease Clinic, University of Siena, Siena, Italy.; Azienda Ospedaliero-Universitaria Senese [European Reference Network (ERN) for Rare Immunodeficiency, Autoinflammatory and Autoimmune Diseases (RITA) Center] Siena, Italy., Tufan A; Department of Internal Medicine, Division of Rheumatology, Gazi University Hospital, Ankara, Turkey., Ragab G; Internal Medicine Department, Rheumatology and Clinical Immunology Unit, Faculty of Medicine, Cairo University, Giza, Egypt.; 6th of October City, Egypt Faculty of Medicine, Faculty of Medicine, Newgiza University., Lopalco G; Department of Precision and Regenerative Medicine and Ionian Area (DiMePRe-J) Policlinic Hospital, University of Bari, Bari, Italy., Portincasa P; Clinica Medica 'A. Murri', Division of Internal Medicine, Department of Precision and Regenerative Medicine and Ionian Area (DiMePre-J), University of Bari Aldo Moro, Bari, Italy., Rigante D; Department of Life Sciences and Public Health, Fondazione Policlinico Universitario A. Gemelli IRCCS, Rome, Italy.; Periodic Fever Research Center, Università Cattolica Sacro Cuore, Rome, Italy., Al-Mayouf SM; Department of Pediatrics, King Faisal Specialist Hospital and Research Center, College of Medicine, Alfaisal University, Riyadh, Saudi Arabia., Şahin A; Division of Rheumatology, Department of Internal Medicine, Sivas Cumhuriyet University Medical Faculty, Sivas, Turkey., Tekgöz N; Division of Pediatric Rheumatology, Ankara Etilik Hospital City Hospital, Ankara, Turkey., Verrecchia E; Periodic Fever Research Center, Università Cattolica Sacro Cuore, Rome, Italy.; Department of Aging, Neurological, Orthopedic and Head and Neck Sciences, Fondazione Policlinico Universitario Agostino Gemelli Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS), Rome, Italy., Fotis L; Department of Pediatrics, Attikon General Hospital, National and Kapodistrian University of Athens, Greece., Barone P; Pediatric Rheumatology Unit, Department of integrated Maternal-Child and Reproduction Activity, AOU 'Policlinico-San Marco' Catania, Italy., Sfikakis PP; Joint Academic Rheumatology Program, Medical School, National and Kapodistrian University of Athens, [European Reference Network (ERN) for Rare Immunodeficiency, Autoinflammatory and Autoimmune Diseases (RITA) Center], Athens, Greece., Batu ED; Division of Pediatric Rheumatology, Department of Pediatrics, Hacettepe University School of Medicine, Ankara, Turkey., Gaggiano C; Department of Medical Sciences, Surgery and Neurosciences, Research Center of Systemic Autoinflammatory Diseases and Behçet's Disease Clinic, University of Siena, Siena, Italy.; Azienda Ospedaliero-Universitaria Senese [European Reference Network (ERN) for Rare Immunodeficiency, Autoinflammatory and Autoimmune Diseases (RITA) Center] Siena, Italy., Ozen S; Division of Pediatric Rheumatology, Department of Pediatrics, Hacettepe University School of Medicine, Ankara, Turkey., Bes C; Department of Rheumatology, University of Health Sciences Başakşehir Çam and Sakura City Hospital, Istanbul, Turkey., Akay N; Department of Paediatrics, Division of Paediatric Rheumatology, Istanbul University-Cerrahpasa, Faculty of Medicine, Istanbul, Turkey., Konte EK; Department of Paediatrics, Division of Paediatric Rheumatology, Istanbul University-Cerrahpasa, Faculty of Medicine, Istanbul, Turkey., Aslan E; Department of Paediatrics, Division of Paediatric Rheumatology, Istanbul University-Cerrahpasa, Faculty of Medicine, Istanbul, Turkey., Torunoglu Z; Department of Paediatrics, Division of Paediatric Rheumatology, Istanbul University-Cerrahpasa, Faculty of Medicine, Istanbul, Turkey., Karakaya B; Department of Internal Medicine, Division of Rheumatology, Gazi University Hospital, Ankara, Turkey., Yildirim D; Department of Internal Medicine, Division of Rheumatology, Gazi University Hospital, Ankara, Turkey., Kucuk H; Department of Internal Medicine, Division of Rheumatology, Gazi University Hospital, Ankara, Turkey., Noto A; Clinica Medica 'A. Murri', Division of Internal Medicine, Department of Precision and Regenerative Medicine and Ionian Area (DiMePre-J), University of Bari Aldo Moro, Bari, Italy., Khalil M; Clinica Medica 'A. Murri', Division of Internal Medicine, Department of Precision and Regenerative Medicine and Ionian Area (DiMePre-J), University of Bari Aldo Moro, Bari, Italy., Sicignano LL; Department of Aging, Neurological, Orthopedic and Head and Neck Sciences, Fondazione Policlinico Universitario Agostino Gemelli Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS), Rome, Italy., Alsaleem A; Department of Pediatrics, King Faisal Specialist Hospital and Research Center, College of Medicine, Alfaisal University, Riyadh, Saudi Arabia., Alsonbul A; Department of Pediatrics, King Faisal Specialist Hospital and Research Center, College of Medicine, Alfaisal University, Riyadh, Saudi Arabia., Babayiğit A; Division of Rheumatology, Department of Internal Medicine, Sivas Cumhuriyet University Medical Faculty, Sivas, Turkey., Semanur E; Division of Pediatric Rheumatology, Ankara Etilik Hospital City Hospital, Ankara, Turkey., Kourtesi K; Department of Pediatrics, Attikon General Hospital, National and Kapodistrian University of Athens, Greece., Papa S; Pediatric Rheumatology Unit, Department of integrated Maternal-Child and Reproduction Activity, AOU 'Policlinico-San Marco' Catania, Italy., Laskari K; Joint Academic Rheumatology Program, Medical School, National and Kapodistrian University of Athens, [European Reference Network (ERN) for Rare Immunodeficiency, Autoinflammatory and Autoimmune Diseases (RITA) Center], Athens, Greece., Deniz R; Department of Rheumatology, University of Health Sciences Başakşehir Çam and Sakura City Hospital, Istanbul, Turkey., Alemanno A; Department of Medical Sciences, Surgery and Neurosciences, Research Center of Systemic Autoinflammatory Diseases and Behçet's Disease Clinic, University of Siena, Siena, Italy.; Azienda Ospedaliero-Universitaria Senese [European Reference Network (ERN) for Rare Immunodeficiency, Autoinflammatory and Autoimmune Diseases (RITA) Center] Siena, Italy., Maggio MC; University Department of Health Promotion, Mother and Child Care, Internal Medicine and Medical Specialties (PROMISE) 'G. D'Alessandro', University of Palermo, Palermo, Italy., Hernández-Rodríguez J; Department of Autoimmune Diseases, Institut d'Investigacions Biomèdiques August Pi I Sunyer (IDIBAPS), Hospital Clínic of Barcelona [European Reference Network (ERN) for Rare Immunodeficiency, Autoinflammatory and Autoimmune Diseases (RITA) Center], University of Barcelona, Barcelona, Spain., Gomez-Caverzaschi V; Department of Autoimmune Diseases, Institut d'Investigacions Biomèdiques August Pi I Sunyer (IDIBAPS), Hospital Clínic of Barcelona [European Reference Network (ERN) for Rare Immunodeficiency, Autoinflammatory and Autoimmune Diseases (RITA) Center], University of Barcelona, Barcelona, Spain., De Paulis A; Department of Translational Medical Sciences, Section of Clinical Immunology, University of Naples Federico II, Naples, Italy, Center for Basic and Clinical Immunology Research (CISI), WAO Center of Excellence, University of Naples Federico II, Naples, Italy., Mormile I; Department of Translational Medical Sciences, Section of Clinical Immunology, University of Naples Federico II, Naples, Italy, Center for Basic and Clinical Immunology Research (CISI), WAO Center of Excellence, University of Naples Federico II, Naples, Italy., Aragona E; Division of Gastroenterology, Ospedali Riuniti Villa Sofia-Vincenzo Cervello, Palermo, Italy., Bronte F; Division of Gastroenterology, Ospedali Riuniti Villa Sofia-Vincenzo Cervello, Palermo, Italy., Gallizzi R; Pediatric Rheumatology, Department of Health Sciences, Magna Graecia University, Catanzaro, Italy., Insalaco A; Division of Rheumatology, IRCCS Ospedale Pediatrico Bambino Gesù, Rome, Italy., Olivieri AN; Department of Woman, Child and of General and Specialized Surgery, University of Campania ``Luigi Vanvitelli'', Naples, Italy., Bilgin E; Faculty of Medicine, Division of Rheumatology, Sakarya University, Sakarya, Turkey., Erdik N; Faculty of Medicine, Division of Rheumatology, Sakarya University, Sakarya, Turkey., Saad MA; Internal Medicine Department, Rheumatology and Clinical Immunology Unit, Faculty of Medicine, Cairo University, Giza, Egypt., Robles-Marhuenda Á; Department of Internal Medicine, Autoimmune Disease Unit, Hospital Universitario La Paz, Madrid, Spain., Lo Gullo A; Unit of Rheumatology, Department of Medicine, ARNAS Garibaldi Hospital, Catania, Italy., Conforti A; Ospedale San Paolo di Civitavecchia, U.O. Medicina Generale, Civitavecchia, Rome, Italy., Tornero Romero F; Internal Medicine Department, Hospital Universitario Fundación Jiménez Díaz, Madrid, Spain., Ogunjimi B; Antwerp Center for Translational Immunology and Virology (ACTIV), Center for Health Economics Research and Modeling Infectious Diseases (CHERMID), Vaccine and Infectious Disease Institute (VAXINFECTIO), University of Antwerp, Antwerp, Belgium.; Division of Paediatric Rheumatology, Department of Paediatrics, Antwerp University Hospital (UZA), Antwerp, Belgium.; Division of Paediatric Rheumatology, Department of Paediatrics, Kidz Health Castle Universitair Ziekenhuis Brussel (UZB), Jette, Belgium.; Division of Paediatric Rheumatology, Department of Rheumatology, Ziekenhuis Aan de Stroom (ZAS), Antwerp, Belgium., Sener S; Division of Pediatric Rheumatology, Department of Pediatrics, Hacettepe University School of Medicine, Ankara, Turkey., Frassi M; Rheumatology and Clinical Immunology, Spedali Civili and Department of Clinical and Experimental Sciences, University of Brescia, [European Reference Network (ERN) for Rare Immunodeficiency, Autoinflammatory and Autoimmune Diseases (RITA) Center], Brescia, Italy., Conti G; Pediatric Nephrology and Rheumatology Unit, Azienda Ospedaliero Universitaria (AOU) G Martino, Messina, Italy., Cauli A; Rheumatology Unit, Department of Medical Sciences and Public health, University and AOU of Cagliari, Cagliari, Italy., Govoni M; Rheumatology Unit, Department of Medical Sciences, Azienda Ospedaliero-Universitaria S. Anna-Ferrara, University of Ferrara, Ferrara, Italy., Marzano AV; Dermatology Unit, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.; Department of Pathophysiology and Transplantation, Università Degli Studi di Milano, Milan, Italy., Moltrasio C; Dermatology Unit, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.; Department of Pathophysiology and Transplantation, Università Degli Studi di Milano, Milan, Italy., Więsik-Szewczyk E; Department of Internal Medicine, Pneumonology, Allergology and Clinical Immunology, Central Clinical Hospital of the Ministry of National Defense, Military Institute of Medicine, National Research Institute, Warsaw, Poland., Tharwat S; Rheumatology and Immunology Unit, Internal Medicine Department, Mansoura University, Mansoura, Egypt.; Department of Internal Medicine, Faculty of Medicine, Horus University, New Damietta, Egypt., Moshrif A; Rheumatology Department, Faculty of Medicine, Al-Azhar University, Assuit, Egypt., Karamanakos A; Department of Rheumatology, 'Evangelismos' General Hospital, Athens, Greece., Semanur E; Samsun Training and Research Hospital, İlkadım/Samsun, Turkey., Balistreri A; Azienda Ospedaliero-Universitaria Senese [European Reference Network (ERN) for Rare Immunodeficiency, Autoinflammatory and Autoimmune Diseases (RITA) Center] Siena, Italy.; Bioengineering and Biomedical Data Science Lab, Department of Medical Biotechnologies, University of Siena, Siena, Italy., Frediani B; Department of Medical Sciences, Surgery and Neurosciences, Research Center of Systemic Autoinflammatory Diseases and Behçet's Disease Clinic, University of Siena, Siena, Italy.; Azienda Ospedaliero-Universitaria Senese [European Reference Network (ERN) for Rare Immunodeficiency, Autoinflammatory and Autoimmune Diseases (RITA) Center] Siena, Italy., Fabiani C; Azienda Ospedaliero-Universitaria Senese [European Reference Network (ERN) for Rare Immunodeficiency, Autoinflammatory and Autoimmune Diseases (RITA) Center] Siena, Italy.; Ophthalmology Unit, Department of Medicine, Surgery and Neurosciences, University of Siena, Siena, Italy., Kasapçopur Ö; Department of Paediatrics, Division of Paediatric Rheumatology, Istanbul University-Cerrahpasa, Faculty of Medicine, Istanbul, Turkey., Cantarini L; Department of Medical Sciences, Surgery and Neurosciences, Research Center of Systemic Autoinflammatory Diseases and Behçet's Disease Clinic, University of Siena, Siena, Italy.; Azienda Ospedaliero-Universitaria Senese [European Reference Network (ERN) for Rare Immunodeficiency, Autoinflammatory and Autoimmune Diseases (RITA) Center] Siena, Italy.
Source: Rheumatology (Oxford, England) [Rheumatology (Oxford)] 2026 Jul 13. Date of Electronic Publication: 2026 Jul 13.
Publication Type: Journal Article
Journal Info: Publisher: Oxford University Press Country of Publication: England NLM ID: 100883501 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1462-0332 (Electronic) Linking ISSN: 14620324 NLM ISO Abbreviation: Rheumatology (Oxford) Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1462-0332
DOI:10.1093/rheumatology/keag361