| Authors: |
Reddy SR; BioMarin Pharmaceutical Inc., 770 Lindaro Street, San Rafael, CA, 94901, USA. Electronic address: Sheila.Reddy@bmrn.com., Pimenta JM; BioMarin (UK) Ltd, 10 Bloomsbury Way, London, WC1A 2SL, UK. Electronic address: Jeanne.Pimenta@bmrn.com., Shepherd H; Clinical Practice Research Datalink (CPRD), Medicines and Healthcare products Regulatory Agency (MHRA), 10 South Colonnade, Canary Wharf, London, UK. Electronic address: Hilary.Shepherd@mhra.gov.uk., Sutton J; BioMarin (UK) Ltd, 10 Bloomsbury Way, London, WC1A 2SL, UK. Electronic address: jaim.sutton@gmail.com., Cheung M; NIHR Great Ormond Street Hospital Biomedical Research Centre, University College London, Guilford St, London, WC1N 3BH, UK. Electronic address: moira.cheung@gosh.nhs.uk., Irving M; Myriad Trials, 3-4 Devonshire Street, London, W1W 5DT, UK. Electronic address: melita@myriadtrials.com., Mukherjee S; BioMarin (UK) Ltd, 10 Bloomsbury Way, London, WC1A 2SL, UK. Electronic address: swati.mukherjee@bmrn.com., Axson EL; Clinical Practice Research Datalink (CPRD), Medicines and Healthcare products Regulatory Agency (MHRA), 10 South Colonnade, Canary Wharf, London, UK. Electronic address: Eleanor.Axson@mhra.gov.uk., Williams R; Clinical Practice Research Datalink (CPRD), Medicines and Healthcare products Regulatory Agency (MHRA), 10 South Colonnade, Canary Wharf, London, UK. Electronic address: Rachael.Williams@mhra.gov.uk. |