Liver-directed neonatal gene therapy prevents cardiac, bone, ear, and eye disease in mucopolysaccharidosis I mice
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| Title: | Liver-directed neonatal gene therapy prevents cardiac, bone, ear, and eye disease in mucopolysaccharidosis I mice |
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| Authors: | Liu, Yuli1, Xu, Lingfei1, Hennig, Anne K.1, Kovacs, Attila1, Fu, Annabel1, Chung, Sarah1, Lee, David1, Wang, Bin1, Herati, Ramin S.1, Mosinger Ogilvie, Judith2, Cai, Shi-Rong1, Parker Ponder, Katherine1,3 kponder@im.wustl.edu |
| Source: | Molecular Therapy. Jan2005, Vol. 11 Issue 1, p35-47. 13p. |
| Database: | Academic Search Ultimate |
| ISSN: | 15250016 |
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| DOI: | 10.1016/j.ymthe.2004.08.027 |