The Placebo Effect in Rare Disease Clinical Trials: Measurement, Impact, and Statistical Approaches for Patient‐as‐Own‐Control Designs.

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Bibliographic Details
Title: The Placebo Effect in Rare Disease Clinical Trials: Measurement, Impact, and Statistical Approaches for Patient‐as‐Own‐Control Designs.
Authors: Summar, Marshall L.1,2 (AUTHOR) msummar@uncommoncures.com, Woodcock, Janet3 (AUTHOR)
Source: CTS: Clinical & Translational Science. May2026, Vol. 19 Issue 5, p1-18. 18p.
Database: Academic Search Ultimate
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Description
ISSN:17528054
DOI:10.1111/cts.70550