Burosumab vs conventional therapy in children with X-linked hypophosphatemia: results of the open-label, phase 3 extension period.

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Title: Burosumab vs conventional therapy in children with X-linked hypophosphatemia: results of the open-label, phase 3 extension period.
Authors: Ward LM; Department of Pediatrics, Faculty of Medicine, University of Ottawa, Ottawa, Ontario, K1H 8L1, Canada., Högler W; Department of Paediatrics and Adolescent Medicine, Johannes Kepler University Linz, 4040 Linz, Austria.; Institute of Metabolism and Systems Research, University of Birmingham, Edgbaston, Birmingham, B15 2TT, United Kingdom., Glorieux FH; Department of Surgery, Pediatrics, and Human Genetics, Shriners Hospitals for Children and McGill University, Montreal, Quebec, H4A 0A9, Canada., Portale AA; Department of Pediatrics, University of California, San Francisco, CA, 94158, United States., Whyte MP; Shriners Hospitals for Children St Louis, St Louis, MO, 63110, United States., Munns CF; Faculty of Medicine, The University of Queensland, Brisbane, Queensland, 4072, Australia.; Faculty of Medicine, Child Health Research Centre, The University of Queensland, Brisbane, Queensland, 4072, Australia.; Department of Endocrinology and Diabetes, Queensland Children's Hospital, Brisbane, Queensland, 4072, Australia., Nilsson O; Division of Pediatric Endocrinology, Department of Women's and Children's Health, Center for Molecular Medicine, Karolinska Institutet and University Hospital, SE-17176 Stockholm, Sweden.; Department of Pediatrics, School of Medical Sciences, Örebro University and University Hospital, S-701 82 Örebro, Sweden., Simmons JH; Division of Endocrinology and Diabetes, Department of Pediatrics, Vanderbilt University School of Medicine, Vanderbilt University, Nashville, TN, 37232, United States., Padidela R; Department of Paediatric Endocrinology, Royal Manchester Children's Hospital, Manchester, M13 9WL, United Kingdom., Namba N; Department of Pediatrics, Osaka Hospital, Japan Community Healthcare Organization, Osaka, 553-0003, Japan.; Osaka University Graduate School of Medicine, Osaka, 565-0871, Japan., Cheong HI; Department of Pediatrics, Hallym University Sacred Heart Hospital, Dongan-gu, Anyang, 14068, South Korea., Sochett E; Department of Pediatrics, Hospital for Sick Children, Toronto, Ontario, M5G 1E8, Canada., Muroya K; Department of Endocrinology, Kanagawa Children's Medical Center, Yokohama, Kanagawa 232-0066, Japan., Tanaka H; Division of Pediatrics, Okayama Saiseikai General Hospital Outpatient Center, Kita-ku, Okayama, 700-8511, Japan., Pitukcheewanont P; Center of Endocrinology, Diabetes and Metabolism, Children's Hospital of Los Angeles, Los Angeles, CA, 90027, United States., Gottesman GS; Shriners Hospitals for Children St Louis, St Louis, MO, 63110, United States., Biggin A; Department of Endocrinology, The University of Sydney Children's Hospital Westmead Clinical School, The Children's Hospital at Westmead, Westmead, New South Wales, 2145, Australia., Perwad F; Department of Pediatrics, University of California, San Francisco, CA, 94158, United States., Chen A; Ultragenyx Pharmaceutical Inc., Novato, CA, 94949, United States., Lawrence Merritt Ii J; Ultragenyx Pharmaceutical Inc., Novato, CA, 94949, United States., Imel EA; Department of Medicine, Indiana University School of Medicine, Indianapolis, IN, 46202, United States.
Source: JBMR plus [JBMR Plus] 2024 Jan 04; Vol. 8 (1), pp. ziad001. Date of Electronic Publication: 2024 Jan 04 (Print Publication: 2024).
Publication Type: Clinical Trial; Journal Article
Journal Info: Publisher: Oxford University Press Country of Publication: England NLM ID: 101707013 Publication Model: eCollection Cited Medium: Internet ISSN: 2473-4039 (Electronic) Linking ISSN: 24734039 NLM ISO Abbreviation: JBMR Plus Subsets: PubMed not MEDLINE
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  Data: Burosumab vs conventional therapy in children with X-linked hypophosphatemia: results of the open-label, phase 3 extension period.
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  Data: <searchLink fieldCode="AU" term="%22Ward+LM%22">Ward LM</searchLink>; Department of Pediatrics, Faculty of Medicine, University of Ottawa, Ottawa, Ontario, K1H 8L1, Canada.<br /><searchLink fieldCode="AU" term="%22Högler+W%22">Högler W</searchLink>; Department of Paediatrics and Adolescent Medicine, Johannes Kepler University Linz, 4040 Linz, Austria.; Institute of Metabolism and Systems Research, University of Birmingham, Edgbaston, Birmingham, B15 2TT, United Kingdom.<br /><searchLink fieldCode="AU" term="%22Glorieux+FH%22">Glorieux FH</searchLink>; Department of Surgery, Pediatrics, and Human Genetics, Shriners Hospitals for Children and McGill University, Montreal, Quebec, H4A 0A9, Canada.<br /><searchLink fieldCode="AU" term="%22Portale+AA%22">Portale AA</searchLink>; Department of Pediatrics, University of California, San Francisco, CA, 94158, United States.<br /><searchLink fieldCode="AU" term="%22Whyte+MP%22">Whyte MP</searchLink>; Shriners Hospitals for Children St Louis, St Louis, MO, 63110, United States.<br /><searchLink fieldCode="AU" term="%22Munns+CF%22">Munns CF</searchLink>; Faculty of Medicine, The University of Queensland, Brisbane, Queensland, 4072, Australia.; Faculty of Medicine, Child Health Research Centre, The University of Queensland, Brisbane, Queensland, 4072, Australia.; Department of Endocrinology and Diabetes, Queensland Children's Hospital, Brisbane, Queensland, 4072, Australia.<br /><searchLink fieldCode="AU" term="%22Nilsson+O%22">Nilsson O</searchLink>; Division of Pediatric Endocrinology, Department of Women's and Children's Health, Center for Molecular Medicine, Karolinska Institutet and University Hospital, SE-17176 Stockholm, Sweden.; Department of Pediatrics, School of Medical Sciences, Örebro University and University Hospital, S-701 82 Örebro, Sweden.<br /><searchLink fieldCode="AU" term="%22Simmons+JH%22">Simmons JH</searchLink>; Division of Endocrinology and Diabetes, Department of Pediatrics, Vanderbilt University School of Medicine, Vanderbilt University, Nashville, TN, 37232, United States.<br /><searchLink fieldCode="AU" term="%22Padidela+R%22">Padidela R</searchLink>; Department of Paediatric Endocrinology, Royal Manchester Children's Hospital, Manchester, M13 9WL, United Kingdom.<br /><searchLink fieldCode="AU" term="%22Namba+N%22">Namba N</searchLink>; Department of Pediatrics, Osaka Hospital, Japan Community Healthcare Organization, Osaka, 553-0003, Japan.; Osaka University Graduate School of Medicine, Osaka, 565-0871, Japan.<br /><searchLink fieldCode="AU" term="%22Cheong+HI%22">Cheong HI</searchLink>; Department of Pediatrics, Hallym University Sacred Heart Hospital, Dongan-gu, Anyang, 14068, South Korea.<br /><searchLink fieldCode="AU" term="%22Sochett+E%22">Sochett E</searchLink>; Department of Pediatrics, Hospital for Sick Children, Toronto, Ontario, M5G 1E8, Canada.<br /><searchLink fieldCode="AU" term="%22Muroya+K%22">Muroya K</searchLink>; Department of Endocrinology, Kanagawa Children's Medical Center, Yokohama, Kanagawa 232-0066, Japan.<br /><searchLink fieldCode="AU" term="%22Tanaka+H%22">Tanaka H</searchLink>; Division of Pediatrics, Okayama Saiseikai General Hospital Outpatient Center, Kita-ku, Okayama, 700-8511, Japan.<br /><searchLink fieldCode="AU" term="%22Pitukcheewanont+P%22">Pitukcheewanont P</searchLink>; Center of Endocrinology, Diabetes and Metabolism, Children's Hospital of Los Angeles, Los Angeles, CA, 90027, United States.<br /><searchLink fieldCode="AU" term="%22Gottesman+GS%22">Gottesman GS</searchLink>; Shriners Hospitals for Children St Louis, St Louis, MO, 63110, United States.<br /><searchLink fieldCode="AU" term="%22Biggin+A%22">Biggin A</searchLink>; Department of Endocrinology, The University of Sydney Children's Hospital Westmead Clinical School, The Children's Hospital at Westmead, Westmead, New South Wales, 2145, Australia.<br /><searchLink fieldCode="AU" term="%22Perwad+F%22">Perwad F</searchLink>; Department of Pediatrics, University of California, San Francisco, CA, 94158, United States.<br /><searchLink fieldCode="AU" term="%22Chen+A%22">Chen A</searchLink>; Ultragenyx Pharmaceutical Inc., Novato, CA, 94949, United States.<br /><searchLink fieldCode="AU" term="%22Lawrence+Merritt+Ii+J%22">Lawrence Merritt Ii J</searchLink>; Ultragenyx Pharmaceutical Inc., Novato, CA, 94949, United States.<br /><searchLink fieldCode="AU" term="%22Imel+EA%22">Imel EA</searchLink>; Department of Medicine, Indiana University School of Medicine, Indianapolis, IN, 46202, United States.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Oxford+University+Press%22">Oxford University Press </searchLink><i>Country of Publication: </i>England <i>NLM ID: </i>101707013 <i>Publication Model: </i>eCollection <i>Cited Medium: </i>Internet <i>ISSN: </i>2473-4039 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2224734039%22">24734039 </searchLink><i>NLM ISO Abbreviation: </i>JBMR Plus <i>Subsets: </i>PubMed not MEDLINE
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