Trial-ready external controls for gene therapy: The MATCH cohort in maple syrup urine disease.
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| Title: | Trial-ready external controls for gene therapy: The MATCH cohort in maple syrup urine disease. |
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| Authors: | Brigatti KW; Clinic for Special Children, Gordonville, PA 17529, USA., Rodrigues A; Clinic for Special Children, Gordonville, PA 17529, USA., Sweigert E; Clinic for Special Children, Gordonville, PA 17529, USA., Williamson J; Clinic for Special Children, Gordonville, PA 17529, USA., Koehler A; Clinic for Special Children, Gordonville, PA 17529, USA., Meier GL; Clinic for Special Children, Gordonville, PA 17529, USA., Poskitt LE; Clinic for Special Children, Gordonville, PA 17529, USA., Carson VJ; Clinic for Special Children, Gordonville, PA 17529, USA., Robinson D; Clinic for Special Children, Gordonville, PA 17529, USA., Strauss KA; Clinic for Special Children, Gordonville, PA 17529, USA; Plowshare Therapies, Lancaster, PA 17603, USA. Electronic address: kastrauss@plowsharetherapies.com. |
| Source: | Cell reports. Medicine [Cell Rep Med] 2026 Jun 16; Vol. 7 (6), pp. 102799. Date of Electronic Publication: 2026 May 12. |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Cell Press Country of Publication: United States NLM ID: 101766894 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2666-3791 (Electronic) Linking ISSN: 26663791 NLM ISO Abbreviation: Cell Rep Med Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 42127902 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Trial-ready external controls for gene therapy: The MATCH cohort in maple syrup urine disease. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Brigatti+KW%22">Brigatti KW</searchLink>; Clinic for Special Children, Gordonville, PA 17529, USA.<br /><searchLink fieldCode="AU" term="%22Rodrigues+A%22">Rodrigues A</searchLink>; Clinic for Special Children, Gordonville, PA 17529, USA.<br /><searchLink fieldCode="AU" term="%22Sweigert+E%22">Sweigert E</searchLink>; Clinic for Special Children, Gordonville, PA 17529, USA.<br /><searchLink fieldCode="AU" term="%22Williamson+J%22">Williamson J</searchLink>; Clinic for Special Children, Gordonville, PA 17529, USA.<br /><searchLink fieldCode="AU" term="%22Koehler+A%22">Koehler A</searchLink>; Clinic for Special Children, Gordonville, PA 17529, USA.<br /><searchLink fieldCode="AU" term="%22Meier+GL%22">Meier GL</searchLink>; Clinic for Special Children, Gordonville, PA 17529, USA.<br /><searchLink fieldCode="AU" term="%22Poskitt+LE%22">Poskitt LE</searchLink>; Clinic for Special Children, Gordonville, PA 17529, USA.<br /><searchLink fieldCode="AU" term="%22Carson+VJ%22">Carson VJ</searchLink>; Clinic for Special Children, Gordonville, PA 17529, USA.<br /><searchLink fieldCode="AU" term="%22Robinson+D%22">Robinson D</searchLink>; Clinic for Special Children, Gordonville, PA 17529, USA.<br /><searchLink fieldCode="AU" term="%22Strauss+KA%22">Strauss KA</searchLink>; Clinic for Special Children, Gordonville, PA 17529, USA; Plowshare Therapies, Lancaster, PA 17603, USA. Electronic address: kastrauss@plowsharetherapies.com. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22101766894%22">Cell reports. Medicine</searchLink> [Cell Rep Med] 2026 Jun 16; Vol. 7 (6), pp. 102799. <i>Date of Electronic Publication: </i>2026 May 12. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Cell+Press%22">Cell Press </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101766894 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>2666-3791 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2226663791%22">26663791 </searchLink><i>NLM ISO Abbreviation: </i>Cell Rep Med <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=42127902 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1016/j.xcrm.2026.102799 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: 102799 Titles: – TitleFull: Trial-ready external controls for gene therapy: The MATCH cohort in maple syrup urine disease. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Brigatti KW – PersonEntity: Name: NameFull: Rodrigues A – PersonEntity: Name: NameFull: Sweigert E – PersonEntity: Name: NameFull: Williamson J – PersonEntity: Name: NameFull: Koehler A – PersonEntity: Name: NameFull: Meier GL – PersonEntity: Name: NameFull: Poskitt LE – PersonEntity: Name: NameFull: Carson VJ – PersonEntity: Name: NameFull: Robinson D – PersonEntity: Name: NameFull: Strauss KA IsPartOfRelationships: – BibEntity: Dates: – D: 16 M: 06 Text: 2026 Jun 16 Type: published Y: 2026 Identifiers: – Type: issn-electronic Value: 2666-3791 Numbering: – Type: volume Value: 7 – Type: issue Value: 6 Titles: – TitleFull: Cell reports. Medicine Type: main |
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