Trial-ready external controls for gene therapy: The MATCH cohort in maple syrup urine disease.

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Title: Trial-ready external controls for gene therapy: The MATCH cohort in maple syrup urine disease.
Authors: Brigatti KW; Clinic for Special Children, Gordonville, PA 17529, USA., Rodrigues A; Clinic for Special Children, Gordonville, PA 17529, USA., Sweigert E; Clinic for Special Children, Gordonville, PA 17529, USA., Williamson J; Clinic for Special Children, Gordonville, PA 17529, USA., Koehler A; Clinic for Special Children, Gordonville, PA 17529, USA., Meier GL; Clinic for Special Children, Gordonville, PA 17529, USA., Poskitt LE; Clinic for Special Children, Gordonville, PA 17529, USA., Carson VJ; Clinic for Special Children, Gordonville, PA 17529, USA., Robinson D; Clinic for Special Children, Gordonville, PA 17529, USA., Strauss KA; Clinic for Special Children, Gordonville, PA 17529, USA; Plowshare Therapies, Lancaster, PA 17603, USA. Electronic address: kastrauss@plowsharetherapies.com.
Source: Cell reports. Medicine [Cell Rep Med] 2026 Jun 16; Vol. 7 (6), pp. 102799. Date of Electronic Publication: 2026 May 12.
Publication Type: Journal Article
Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 101766894 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2666-3791 (Electronic) Linking ISSN: 26663791 NLM ISO Abbreviation: Cell Rep Med Subsets: MEDLINE
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  Data: <searchLink fieldCode="AU" term="%22Brigatti+KW%22">Brigatti KW</searchLink>; Clinic for Special Children, Gordonville, PA 17529, USA.<br /><searchLink fieldCode="AU" term="%22Rodrigues+A%22">Rodrigues A</searchLink>; Clinic for Special Children, Gordonville, PA 17529, USA.<br /><searchLink fieldCode="AU" term="%22Sweigert+E%22">Sweigert E</searchLink>; Clinic for Special Children, Gordonville, PA 17529, USA.<br /><searchLink fieldCode="AU" term="%22Williamson+J%22">Williamson J</searchLink>; Clinic for Special Children, Gordonville, PA 17529, USA.<br /><searchLink fieldCode="AU" term="%22Koehler+A%22">Koehler A</searchLink>; Clinic for Special Children, Gordonville, PA 17529, USA.<br /><searchLink fieldCode="AU" term="%22Meier+GL%22">Meier GL</searchLink>; Clinic for Special Children, Gordonville, PA 17529, USA.<br /><searchLink fieldCode="AU" term="%22Poskitt+LE%22">Poskitt LE</searchLink>; Clinic for Special Children, Gordonville, PA 17529, USA.<br /><searchLink fieldCode="AU" term="%22Carson+VJ%22">Carson VJ</searchLink>; Clinic for Special Children, Gordonville, PA 17529, USA.<br /><searchLink fieldCode="AU" term="%22Robinson+D%22">Robinson D</searchLink>; Clinic for Special Children, Gordonville, PA 17529, USA.<br /><searchLink fieldCode="AU" term="%22Strauss+KA%22">Strauss KA</searchLink>; Clinic for Special Children, Gordonville, PA 17529, USA; Plowshare Therapies, Lancaster, PA 17603, USA. Electronic address: kastrauss@plowsharetherapies.com.
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  Data: <searchLink fieldCode="JN" term="%22101766894%22">Cell reports. Medicine</searchLink> [Cell Rep Med] 2026 Jun 16; Vol. 7 (6), pp. 102799. <i>Date of Electronic Publication: </i>2026 May 12.
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        Value: 10.1016/j.xcrm.2026.102799
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              Text: 2026 Jun 16
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