Meeting report: 2025 muscular dystrophy association summit on 'safety and challenges in gene therapy of neuromuscular diseases'.
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| Title: | Meeting report: 2025 muscular dystrophy association summit on 'safety and challenges in gene therapy of neuromuscular diseases'. |
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| Authors: | Lin BC; Muscular Dystrophy Association, Chicago, IL, USA., Lek A; Muscular Dystrophy Association, Chicago, IL, USA., Bönnemann CG; Department of Genomic and Translational Neuroscience, St. Jude Children's Research Hospital, Memphis, TN, USA., Byrne BJ; Department of Pediatrics and Powell Gene Therapy Center, University of Florida, Gainesville, FL, USA. |
| Source: | Journal of neuromuscular diseases [J Neuromuscul Dis] 2026 Jun 13, pp. 22143602261453651. Date of Electronic Publication: 2026 Jun 13. |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: IOS Press Country of Publication: United States NLM ID: 101649948 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2214-3602 (Electronic) Linking ISSN: 22143599 NLM ISO Abbreviation: J Neuromuscul Dis Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
| ISSN: | 2214-3602 |
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| DOI: | 10.1177/22143602261453651 |